In vivo repopulation ability of genetically corrected bone marrow cells from Fanconi anemia patients

Proceedings of the National Academy of Sciences of the United States of America

Volumn 103, Issue 7, 2006, Pages 2340-2345

  Cohen Haguenauer, Odile ^a,b   Péault, Bruno ^c,d   Bauche, Cécile ^a   Daniel, Marie Thérèse ^b   Casal, Ibrahim ^d   Levy, Vincent ^b   Dausset, Jean ^e   Boiron, Michel ^e   Auclair, Christian ^a   Gluckman, Eliane ^b   Marty, Michel ^b  

^a UNIVERSITÉ PARIS SACLAY   (France)

^b SAINT LOUIS HOSPITAL   (France)

^c CHILDREN S HOSPITAL OF PITTSBURGH   (United States)

^d INSERM   (France)

^e UF de Génétique Moléculaire HÔpital Lariboisière   (France)

Author keywords

Fanconi's anemia; Gene therapy; Heamatopoietic stem cells

Indexed keywords

AMIFOSTINE; COMPLEMENTARY DNA; CYTOKINE; TRIMETAZIDINE;

ADOLESCENT; ANIMAL CELL; ANIMAL MODEL; ARTICLE; BONE MARROW CELL; BONE MARROW CULTURE; CELL GROWTH; CELL POPULATION; CELL SURVIVAL; CELL TRANSPLANTATION; CLONOGENESIS; CONTROLLED STUDY; DNA DAMAGE; FANCONI ANEMIA; GENE THERAPY; GENETIC TRANSDUCTION; GENOMIC INSTABILITY; HEMATOPOIETIC STEM CELL; HUMAN; HUMAN CELL; IN VIVO STUDY; MOUSE; NONHUMAN; OXIDATIVE STRESS; PATHOGENESIS; PRIORITY JOURNAL; RETROVIRUS; SCID MOUSE; TRANSGENE;

ANIMALS; ANTIOXIDANTS; BONE MARROW CELLS; BONE MARROW TRANSPLANTATION; CHILD; DNA, COMPLEMENTARY; FANCONI ANEMIA; FANCONI ANEMIA COMPLEMENTATION GROUP A PROTEIN; FEMALE; GENE THERAPY; HUMANS; MALE; MICE; MICE, INBRED NOD; MICE, SCID; OXIDATIVE STRESS; TRANSFECTION;

ANIMALIA;

EID: 33144486857     PISSN: 00278424     EISSN: None     Source Type: Journal    
DOI: 10.1073/pnas.0510613103     Document Type: Article

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