메뉴 건너뛰기




Volumn 117, Issue 6, 2004, Pages 893-898

Hybrid retroviral vector with MCK enhancers inserted in LTR for stable and specific expression of human factor IX in skeletal muscle

Author keywords

Gene expression; Human factor IX; Hybrid; Muscle specificity; Retroviral vectors

Indexed keywords

BLOOD CLOTTING FACTOR 9; COMPLEMENTARY DNA; CREATINE KINASE; RETROVIRUS VECTOR;

EID: 3242709521     PISSN: 03666999     EISSN: None     Source Type: Journal    
DOI: None     Document Type: Article
Times cited : (4)

References (23)
  • 1
    • 0028386527 scopus 로고
    • Primary myoblast-mediatid gene transfer: Persistent expression of human factor IX in mice
    • Yao SN, Smith KJ, Kurachi K. Primary myoblast-mediatid gene transfer: Persistent expression of human factor IX in mice. Gene Ther 1994;1:99-107.
    • (1994) Gene Ther. , vol.1 , pp. 99-107
    • Yao, S.N.1    Smith, K.J.2    Kurachi, K.3
  • 2
    • 0031040987 scopus 로고    scopus 로고
    • Long-term control of erythropoietin secretion by doxycycline in mice transplanted with engineered primary myoblasts
    • Bohl D, Naffakh N, Heard JM. Long-term control of erythropoietin secretion by doxycycline in mice transplanted with engineered primary myoblasts. Nat Med 1997;3:299-305.
    • (1997) Nat. Med. , vol.3 , pp. 299-305
    • Bohl, D.1    Naffakh, N.2    Heard, J.M.3
  • 3
    • 0027595949 scopus 로고
    • The basic science of gene therapy
    • Mulligan RC. The basic science of gene therapy. Science 1993;260:926-932.
    • (1993) Science , vol.260 , pp. 926-932
    • Mulligan, R.C.1
  • 4
    • 0033856775 scopus 로고    scopus 로고
    • Viral vectors for gene transfer: A review of their use in the treatment of human diseases
    • Walther W, Stein U. Viral vectors for gene transfer: a review of their use in the treatment of human diseases. Drugs 2000; 60:249-271.
    • (2000) Drugs , vol.60 , pp. 249-271
    • Walther, W.1    Stein, U.2
  • 5
    • 0033639189 scopus 로고    scopus 로고
    • Design of retroviral vectors and helper cells for gene therapy
    • Hu WS, Pathak VK. Design of retroviral vectors and helper cells for gene therapy. Pharmacol Rev 2000;52:493-511.
    • (2000) Pharmacol. Rev. , vol.52 , pp. 493-511
    • Hu, W.S.1    Pathak, V.K.2
  • 6
    • 0034633741 scopus 로고    scopus 로고
    • Progress in the Use of Gene Transfer Methods to Treat Genetic Blood Diseases
    • Williams DA, Smith FO. Progress in the Use of Gene Transfer Methods to Treat Genetic Blood Diseases. Hum Gene Ther 2000;11:2059-2066.
    • (2000) Hum. Gene Ther. , vol.11 , pp. 2059-2066
    • Williams, D.A.1    Smith, F.O.2
  • 7
    • 0029818271 scopus 로고    scopus 로고
    • Construction of human factor IX expression vectors in retroviral vector frames optimized for muscle cells
    • Wang JM, Zheng H, Sugahara Y, et al. Construction of human factor IX expression vectors in retroviral vector frames optimized for muscle cells. Hum Gene Ther 1996;7:1743-1756.
    • (1996) Hum. Gene Ther. , vol.7 , pp. 1743-1756
    • Wang, J.M.1    Zheng, H.2    Sugahara, Y.3
  • 8
    • 0030795619 scopus 로고    scopus 로고
    • Persistent systemic production of human factor IX in mice by skeletal myoblast-mediated gene transfer: Feasibility of repeat application to obtain therapeutic levels
    • Wang JM, Zheng H, Blaivas M, et al. Persistent systemic production of human factor IX in mice by skeletal myoblast-mediated gene transfer: feasibility of repeat application to obtain therapeutic levels. Blood 1997;90:1075-1082.
    • (1997) Blood , vol.90 , pp. 1075-1082
    • Wang, J.M.1    Zheng, H.2    Blaivas, M.3
  • 9
    • 0030996011 scopus 로고    scopus 로고
    • Progress in transcriptionally targeted and regulatable vectors for genetic therapy
    • Miller N, Whelan J. Progress in transcriptionally targeted and regulatable vectors for genetic therapy. Hum Gene Ther 1997;8:803-815.
    • (1997) Hum. Gene Ther. , vol.8 , pp. 803-815
    • Miller, N.1    Whelan, J.2
  • 10
    • 0029874105 scopus 로고    scopus 로고
    • Long-term secretion of therapeutic proteins from genetically modified skeletal muscles
    • Naffakh N, Pinset C, Montarras D, et al. Long-term secretion of therapeutic proteins from genetically modified skeletal muscles. Hum Gene Ther 1996;7:11-21.
    • (1996) Hum. Gene Ther. , vol.7 , pp. 11-21
    • Naffakh, N.1    Pinset, C.2    Montarras, D.3
  • 11
    • 0029079981 scopus 로고
    • A retroviral vector containing a muscle-specific enhancer drives gene expression only in differentiated muscle fibers
    • Ferrari G, Salvatori G, Rossi C, et al. A retroviral vector containing a muscle-specific enhancer drives gene expression only in differentiated muscle fibers. Hum Gene Ther 1995;6: 733-742.
    • (1995) Hum. Gene Ther. , vol.6 , pp. 733-742
    • Ferrari, G.1    Salvatori, G.2    Rossi, C.3
  • 12
    • 0031984750 scopus 로고    scopus 로고
    • Exchange of viral promoter/enhancer elements with heterologous regulatory sequences generates targeted hybrid long terminal repeat vectors for gene therapy of melanoma
    • Diaz RM, Eisen T, Hart IR, et al. Exchange of viral promoter/enhancer elements with heterologous regulatory sequences generates targeted hybrid long terminal repeat vectors for gene therapy of melanoma. J Virol 1998;72:789-795.
    • (1998) J. Virol. , vol.72 , pp. 789-795
    • Diaz, R.M.1    Eisen, T.2    Hart, I.R.3
  • 13
    • 0344671602 scopus 로고    scopus 로고
    • Endothelial cell-specific transcriptional targeting from a hybrid long terminal repeat retrovirus vector containing human prepro-endothelin-1 promoter sequences
    • Jager U, Zhao Y, Porter CD. Endothelial cell-specific transcriptional targeting from a hybrid long terminal repeat retrovirus vector containing human prepro-endothelin-1 promoter sequences. J Virol 1999;73:9702-9709.
    • (1999) J. Virol. , vol.73 , pp. 9702-9709
    • Jager, U.1    Zhao, Y.2    Porter, C.D.3
  • 14
    • 0033587651 scopus 로고    scopus 로고
    • Efficient gene transfer by hybrid retroviral vectors to murine spermatogenic cells
    • Danno S, Itoh K, Baum C, et al. Efficient gene transfer by hybrid retroviral vectors to murine spermatogenic cells. Hum Gene Ther 1999;10:1819-1831.
    • (1999) Hum. Gene Ther. , vol.10 , pp. 1819-1831
    • Danno, S.1    Itoh, K.2    Baum, C.3
  • 15
    • 0033135165 scopus 로고    scopus 로고
    • Production of minigene-containing retroviral vectors using an alphavirus/retrovirus hybrid vector system
    • Wahlfors JJ, Morgan RA. Production of minigene-containing retroviral vectors using an alphavirus/retrovirus hybrid vector system. Hum Gene Ther 1999;10:1197-1206.
    • (1999) Hum. Gene Ther. , vol.10 , pp. 1197-1206
    • Wahlfors, J.J.1    Morgan, R.A.2
  • 16
    • 0028900484 scopus 로고
    • Role of intron I in expression of the human factor IX gene
    • Kurachi S, Hitomi Y, Furukawa M, et al. Role of intron I in expression of the human factor IX gene. J Biol Chem 1995; 270:5276-5281.
    • (1995) J. Biol. Chem. , vol.270 , pp. 5276-5281
    • Kurachi, S.1    Hitomi, Y.2    Furukawa, M.3
  • 17
    • 0019856424 scopus 로고
    • Nucleotide sequence of moloney murine leukaemia virus
    • Shinnick TM, Lerner RA, Sutcliffe JG. Nucleotide sequence of moloney murine leukaemia virus. Nature 1981;293:543-548.
    • (1981) Nature , vol.293 , pp. 543-548
    • Shinnick, T.M.1    Lerner, R.A.2    Sutcliffe, J.G.3
  • 18
    • 2642605035 scopus 로고
    • Retroviruses, strategies of replication. The structure and function of retroviral long terminal repeats
    • Swanstrom R. Vogt PK, eds. Germany: Springer-Verlag
    • Majors J. Retroviruses, strategies of replication. The structure and function of retroviral long terminal repeats. In: Swanstrom R. Vogt PK, eds. Germany: Springer-Verlag; 1990:49-92.
    • (1990) , pp. 49-92
    • Majors, J.1
  • 19
    • 0028170357 scopus 로고
    • Retroviral vectors containing chimeric promoter/enhancer elements exhibit cell-type-specific gene expression
    • Couture LA, Mullen CA, Morgan RA. Retroviral vectors containing chimeric promoter/enhancer elements exhibit cell-type-specific gene expression. Hum Gene Ther 1994;5:667-677.
    • (1994) Hum. Gene Ther. , vol.5 , pp. 667-677
    • Couture, L.A.1    Mullen, C.A.2    Morgan, R.A.3
  • 20
    • 0023767237 scopus 로고
    • Design of retrovirus vectors for transfer and expression of the human beta-globin gene
    • Miller AD, Bender MA, Harris EA, et al. Design of retrovirus vectors for transfer and expression of the human beta-globin gene. J Virol 1988;62:4337-4435.
    • (1988) J. Virol. , vol.62 , pp. 4337-4435
    • Miller, A.D.1    Bender, M.A.2    Harris, E.A.3
  • 21
    • 0028978024 scopus 로고
    • Retrovirus-mediated transduction of an engineered intron-containing purine nucleoside phosphorylase gene
    • Jonsson JJ, Habel DE, Mclvor RS. Retrovirus-mediated transduction of an engineered intron-containing purine nucleoside phosphorylase gene. Hum Gene Ther 1995;6:611-623.
    • (1995) Hum. Gene Ther. , vol.6 , pp. 611-623
    • Jonsson, J.J.1    Habel, D.E.2    Mclvor, R.S.3
  • 22
    • 0023911839 scopus 로고
    • Identification of upstream and intragenic regulatory elements that confer cell-type-restricted and differentiation- specific expression on the muscle creatine kinase gene
    • Sternberg EA, Spizz G, Perry WM, et al. Identification of upstream and intragenic regulatory elements that confer cell-type-restricted and differentiation- specific expression on the muscle creatine kinase gene. Mol Cell Biol 1988;8:2896-2909.
    • (1988) Mol. Cell. Biol. , vol.8 , pp. 2896-2909
    • Sternberg, E.A.1    Spizz, G.2    Perry, W.M.3
  • 23
    • 0028303308 scopus 로고
    • The mouse creatine kinase paired E-box element confers muscle-specific expression to a heterologous promoter
    • Martin KA, Walsh K. Mader SL. The mouse creatine kinase paired E-box element confers muscle-specific expression to a heterologous promoter. Gene 1994;142:275-278.
    • (1994) Gene , vol.142 , pp. 275-278
    • Martin, K.A.1    Walsh, K.2    Mader, S.L.3


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.