Unrelated umbilical cord blood transplantation for an infant with β-thalassemia major

Journal of Pediatric Hematology/Oncology

Volumn 26, Issue 6, 2004, Pages 382-385

  Hall, Jennifer G ^a   Martin, Paul L ^a   Wood, Susan ^a   Kurtzberg, Joanne ^a  

^a DUKE UNIVERSITY MEDICAL CENTER   (United States)

Author keywords

thalassemia major; Bone marrow transplantation; Umbilical cord blood transplantation; Unrelated donor transplantation

Indexed keywords

AMPHOTERICIN B; BUSULFAN; CYCLOPHOSPHAMIDE; CYCLOSPORIN A; GRANULOCYTE COLONY STIMULATING FACTOR; IMMUNOGLOBULIN G; IMMUNOSUPPRESSIVE AGENT; THYMOCYTE ANTIBODY;

ARTICLE; AUTOIMMUNE HEMOLYTIC ANEMIA; BLOOD DONOR; CASE REPORT; CHILD GROWTH; CHIMERA; COGNITIVE DEVELOPMENT; DONOR CHIMERISM; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HLA MATCHING; HUMAN; INFANT; MALE; PRIORITY JOURNAL; SURVIVAL; THALASSEMIA MAJOR; UMBILICAL CORD BLOOD; UMBILICAL CORD BLOOD TRANSPLANTATION;

BETA-THALASSEMIA; FETAL BLOOD; HEPARIN; HUMANS; INFANT, NEWBORN; MALE; PRENATAL DIAGNOSIS; STEM CELL TRANSPLANTATION; TIME FACTORS; TRANSPLANTATION CHIMERA; TREATMENT OUTCOME;

EID: 2942627262     PISSN: 10774114     EISSN: None     Source Type: Journal    
DOI: 10.1097/00043426-200406000-00010     Document Type: Article

References (16)

1. Dover G, Valle D. Therapy for β-thalassemia: a paradigm for the treatment of genetic disorders. N Engl J Med. 1994;331:609-610.
2. Gaziev J, Lucarelli G. Stem cell transplantation for hemoglobinopathies. Curr Opinion Pediatr. 2003;15:42-51.
3. Forget BG. Thalassemia syndromes. In: Hoffman, ed, Hematology: basic principles and practice. 3rd ed. Oxford: Churchill Livingstone, 2000:488-499.
4. Cheng C, Lu C, Sun H, et al. Successful matched-unrelated bone marrow transplantation in a patient with beta-thalassemia major. J Pediatr Hematol Oncol. 2002;24:579-581.
5. Kelly P, Kurtzberg J, Vichinsky E, et al. Umbilical cord blood stem cells: application for the treatment of patients with hemoglobinopathies. J Pediatr. 1997;130:695-703.
6. Mentzer W. Bone marrow transplantation for hemoglobinopathies. Curr Opin Hematol. 2000;7:95-100.
7. Thomas E, Sanders J, Borgna-Pignatti C, et al. Marrow transplantation for thalassemia. Lancet. 1982;2:227-229.
8. Lucarelli G. Bone marrow transplantation for thalassemia. J Intern Med. 1997;242:49-52.
9. Lucarelli G, Galimberti M, Polchi P, et al. Bone marrow transplantation in patients with thalassemia. N Engl J Med. 1990;322:417-421.
10. Lucarelli G, Giardini C, Baronciani D. Bone marrow transplantation in thalassemia. Sem Hematol. 1995;32:297-303.
11. Issaragrisil S, Visuthisakchai S, Suvatte V, et al. Brief report: transplantation of cord blood stem cells into a patient with severe thalassemia. N Engl J Med. 1995;332:367-369.
12. Miniero R, Rocha V, Saracco P, et al. Cord blood transplantation in hemoglobinopathies. Bone Marrow Transplant. 1998;22:S78-S79.
13. Locatelli F, Rocha V, Reed W, et al. Related umbilical cord blood transplantation in patients with thalassemia and sickle cell disease. Blood. 2003;101:2137-2143.
14. Rocha V, Wagner J, Sobocinski K, et al. Graft-versus-host-disease in children who have received a cord-blood or bone marrow transplant from an HLA-identical sibling. N Engl J Med. 2000;342:1846-1854.
15. Locatelli F, Rocha V, Chastang C, et al. Factors associated with outcome after cord blood transplantation in children with acute leukemia. Blood. 1999;93:3662-3671.
16. Gluckman E, Rocha V, Boyer-Chammard A, et al. Outcome of cord blood transplantation from related and unrelated donors. N Engl J Med. 1997;337:373-381.