메뉴 건너뛰기




Volumn 15, Issue 1, 2003, Pages 24-31

Stem cell transplantation for hemoglobinopathies

Author keywords

[No Author keywords available]

Indexed keywords

AZATHIOPRINE; BUSULFAN; CYCLOPHOSPHAMIDE; DEFEROXAMINE; FLUDARABINE; HYDROXYUREA; LYMPHOCYTE ANTIBODY; THIOTEPA;

EID: 0037304503     PISSN: 10408703     EISSN: None     Source Type: Journal    
DOI: 10.1097/00008480-200302000-00005     Document Type: Review
Times cited : (59)

References (44)
  • 1
    • 0025070260 scopus 로고
    • Bone marrow transplantation in patients with thalassemia
    • Lucarelli G, Galimberti M, Polchi P, et al.: Bone marrow transplantation in patients with thalassemia. N Engl J Med 1990, 322:417-421. •• The original report of the use of risk classes for transplantation in patients with thalassemia.
    • (1990) N Engl J Med , vol.322 , pp. 417-421
    • Lucarelli, G.1    Galimberti, M.2    Polchi, P.3
  • 2
    • 13344276567 scopus 로고    scopus 로고
    • Marrow transplantation for patients with thalassemia: Results in Class 3 patients
    • Lucarelli G, Clift R, Galimberti M, et al.: Marrow transplantation for patients with thalassemia: results in Class 3 patients. Blood 1996, 87:2082-2088.
    • (1996) Blood , vol.87 , pp. 2082-2088
    • Lucarelli, G.1    Clift, R.2    Galimberti, M.3
  • 3
    • 0012874331 scopus 로고    scopus 로고
    • New preparative regimen for bone marrow transplantation in class 3 young and adult thalassemic patients
    • Sodani P, Gaziev D, Erer B, et al.: New preparative regimen for bone marrow transplantation in class 3 young and adult thalassemic patients. Bone Marrow Transplant 2002, 29(suppl 2):S30. • This abstract provides data on 29 class 3 patients who received BMT following a new preparative regimen. Patients had survival and thalassemia-free survival 96% and 90%, respectively. Transplant-related mortality and rejection were low in these patients.
    • (2002) Bone Marrow Transplant , vol.29 , Issue.SUPPL. 2
    • Sodani, P.1    Gaziev, D.2    Erer, B.3
  • 4
    • 0033558264 scopus 로고    scopus 로고
    • Bone marrow transplantation in adult thalassemic patients
    • Lucarelli G, Galimberti M, Giardini C, et al. Bone marrow transplantation in adult thalassemic patients. Blood 1999, 93:1164-1167.
    • (1999) Blood , vol.93 , pp. 1164-1167
    • Lucarelli, G.1    Galimberti, M.2    Giardini, C.3
  • 5
    • 0030787426 scopus 로고    scopus 로고
    • Current status of allogeneic transplantation for haemoglobinopathies
    • Roberts I. Current status of allogeneic transplantation for haemoglobinopathies [review]. Br J Haematol 1997, 98:1-7.
    • (1997) Br J Haematol , vol.98 , pp. 1-7
    • Roberts, I.1
  • 6
    • 0035905908 scopus 로고    scopus 로고
    • Transplantation of bone marrow as compared with peripheral-blood cells from HLA-identical relatives in patients with hematologic cancers
    • Bensinger WI, Martin PJ, Storer B, et al.: Transplantation of bone marrow as compared with peripheral-blood cells from HLA-identical relatives in patients with hematologic cancers. N Engl J Med 2001, 344:175-181.
    • (2001) N Engl J Med , vol.344 , pp. 175-181
    • Bensinger, W.I.1    Martin, P.J.2    Storer, B.3
  • 7
    • 0035659839 scopus 로고    scopus 로고
    • Peripheral blood stem cell transplantation in children with beta-thalassemia
    • Yesilipek MA, Hazar V, Kupesiz A, et al.: Peripheral blood stem cell transplantation in children with beta-thalassemia. Bone Marrow Transplant 2001, 28:1037-1040.
    • (2001) Bone Marrow Transplant , vol.28 , pp. 1037-1040
    • Yesilipek, M.A.1    Hazar, V.2    Kupesiz, A.3
  • 8
    • 0344925935 scopus 로고    scopus 로고
    • Blood stem cells compared with bone marrow as a source of hematopoietic cells for allogeneic transplantation
    • Champlin R, Schmitz N, Horiwitz MM, et al.: Blood stem cells compared with bone marrow as a source of hematopoietic cells for allogeneic transplantation. Blood 2000, 95:3702-3709.
    • (2000) Blood , vol.95 , pp. 3702-3709
    • Champlin, R.1    Schmitz, N.2    Horiwitz, M.M.3
  • 9
    • 0032945496 scopus 로고    scopus 로고
    • The role of thiotepa in allogeneic bone marrow transplantation for genetic diseases
    • Rosales F, Peylan-Ramu N, Cividalli G, et al.: The role of thiotepa in allogeneic bone marrow transplantation for genetic diseases. Bone Marrow Transplant 1999, 23:861-865.
    • (1999) Bone Marrow Transplant , vol.23 , pp. 861-865
    • Rosales, F.1    Peylan-Ramu, N.2    Cividalli, G.3
  • 10
    • 0034036968 scopus 로고    scopus 로고
    • Bone marrow transplantation from alternative donors for thalassemia: HLA-phenotypically identical relative and HLA-nonidentical sibling or parent transplant
    • Gaziev D, Galimberti M, Lucarelli G, et al.: Bone marrow transplantation from alternative donors for thalassemia: HLA-phenotypically identical relative and HLA-nonidentical sibling or parent transplant. Bone Marrow Transplant 2000, 25:815-821.
    • (2000) Bone Marrow Transplant , vol.25 , pp. 815-821
    • Gaziev, D.1    Galimberti, M.2    Lucarelli, G.3
  • 11
    • 0037097807 scopus 로고    scopus 로고
    • Unrelated donor marrow transplantation for thalassemia: The effect of extended haplotypes
    • La Nasa G, Giardini C, Argiolu F, et al.: Unrelated donor marrow transplantation for thalassemia: the effect of extended haplotypes. Blood 2002, 99:4350-4356. •• This study is the largest published to date on unrelated bone marrow transplantation for β-thalassemia major. The report shows that patients who shared at least one extended haplotype had less acute or chronic GVHD and better survival.
    • (2002) Blood , vol.99 , pp. 4350-4356
    • La Nasa, G.1    Giardini, C.2    Argiolu, F.3
  • 12
    • 0031003083 scopus 로고    scopus 로고
    • Bone marrow and cord blood stem cell transplantation for thalassemia in Thailand
    • Issaragrisil S, Suvatte V, Visudhisakchai S, et al.: Bone marrow and cord blood stem cell transplantation for thalassemia in Thailand. Bone Marrow Transplant 1997, 19(suppl 2):54-56.
    • (1997) Bone Marrow Transplant , vol.19 , Issue.SUPPL. 2 , pp. 54-56
    • Issaragrisil, S.1    Suvatte, V.2    Visudhisakchai, S.3
  • 14
    • 4243913603 scopus 로고    scopus 로고
    • Related cord blood transplant in patients with thalassemia and sickle cell disease
    • Locatelli F, Rocha V, Reed W, et al.: Related cord blood transplant in patients with thalassemia and sickle cell disease. Bone Marrow Transplant 2002, 29(suppl 2):S68. • This abstract provides data on related cord blood transplantation for thalassemia major or sickle cell anemia patients. Although all patients are alive, the incidence of graft failure was higher in thalassemia patients, suggesting that the best immunosuppression before and after transplant has to be determined.
    • (2002) Bone Marrow Transplant , vol.29 , Issue.SUPPL. 2
    • Locatelli, F.1    Rocha, V.2    Reed, W.3
  • 15
    • 0036301696 scopus 로고    scopus 로고
    • The cure of thalassemia by bone marrow transplantation
    • Lucarelli G, Andreani M, Angelucci E: The cure of thalassemia by bone marrow transplantation. Blood Rev 2002, 16:81-85. • This is a more recent update on bone marrow transplantation for thalassemia from the Pesaro BMT Center.
    • (2002) Blood Rev , vol.16 , pp. 81-85
    • Lucarelli, G.1    Andreani, M.2    Angelucci, E.3
  • 16
    • 15844397404 scopus 로고    scopus 로고
    • Persistence of mixed chimerism in patients transplanted for the treatment of thalassemia
    • Andreani M, Manna M, Lucarelli G, et al.: Persistence of mixed chimerism in patients transplanted for the treatment of thalassemia. Blood 1996, 87:3494-3499.
    • (1996) Blood , vol.87 , pp. 3494-3499
    • Andreani, M.1    Manna, M.2    Lucarelli, G.3
  • 17
    • 0033996420 scopus 로고    scopus 로고
    • Long-term survival of ex-thalassemic patients with persistent mixed chimerism after marrow transplantation
    • Andreani M, Nesci S, Lucarelli G, et al.: Long-term survival of ex-thalassemic patients with persistent mixed chimerism after marrow transplantation. Bone Marrow Transplant 2000, 25:401-404.
    • (2000) Bone Marrow Transplant , vol.25 , pp. 401-404
    • Andreani, M.1    Nesci, S.2    Lucarelli, G.3
  • 18
    • 0027438974 scopus 로고
    • Fate of iron stores in thalassemia after bone marrow transplantation
    • Lucarelli G, Angelucci E, Giardini C, et al.: Fate of iron stores in thalassemia after bone marrow transplantation. Lancet 1993, 342:1388-1391.
    • (1993) Lancet , vol.342 , pp. 1388-1391
    • Lucarelli, G.1    Angelucci, E.2    Giardini, C.3
  • 19
    • 0034601375 scopus 로고    scopus 로고
    • Hepatic iron concentration and total body iron stores in thalassemia major
    • Angelucci E, Brittenham GM, McLaren CE, et al.: Hepatic iron concentration and total body iron stores in thalassemia major. N Engl J Med 2000, 343:327-331.
    • (2000) N Engl J Med , vol.343 , pp. 327-331
    • Angelucci, E.1    Brittenham, G.M.2    McLaren, C.E.3
  • 20
    • 0036660189 scopus 로고    scopus 로고
    • Effects of iron overload and hepatitis C virus positivity in determining progression of liver fibrosis in thalassemia following bone marrow transplantation
    • Angelucci E, Muretto P, Nicolucci A, et al.: Effects of iron overload and hepatitis C virus positivity in determining progression of liver fibrosis in thalassemia following bone marrow transplantation. Blood 2002, 100:17-21. • This study provides data on the natural history of liver fibrosis in ex-thalassemics and demonstrates that iron overload and hepatitis C virus are independent risk factors for liver fibrosis progression following transplant.
    • (2002) Blood , vol.100 , pp. 17-21
    • Angelucci, E.1    Muretto, P.2    Nicolucci, A.3
  • 21
    • 0030848104 scopus 로고    scopus 로고
    • Phlebotomy to reduce iron overload in patients cured of thalassemia by bone marrow transplantation
    • Italian Group for Phlebotomy Treatment of Transplanted Thalassemic Patients
    • Angelucci E, Muretto P, Lucarelli G, et al.: Phlebotomy to reduce iron overload in patients cured of thalassemia by bone marrow transplantation. Italian Group for Phlebotomy Treatment of Transplanted Thalassemic Patients. Blood 1997, 90:994-998.
    • (1997) Blood , vol.90 , pp. 994-998
    • Angelucci, E.1    Muretto, P.2    Lucarelli, G.3
  • 22
    • 0032428362 scopus 로고    scopus 로고
    • Evaluation of cardiac status in iron-loaded thalassemia patients following bone marrow transplantation: Improvement in cardiac function during reduction in iron burden
    • Mariotti E, Angelucci E, Agostini A, et al.: Evaluation of cardiac status in iron-loaded thalassemia patients following bone marrow transplantation: improvement in cardiac function during reduction in iron burden. Br J Haematol 1998, 103:916-921.
    • (1998) Br J Haematol , vol.103 , pp. 916-921
    • Mariotti, E.1    Angelucci, E.2    Agostini, A.3
  • 23
    • 0028941571 scopus 로고
    • Desferrioxamine therapy accelerates clearance of iron deposits after bone marrow transplantation for thalassemia
    • Giardini C, Galimberti M, Lucarelli G, et al.: Desferrioxamine therapy accelerates clearance of iron deposits after bone marrow transplantation for thalassemia. Br J Haematol 1995, 89:868-873.
    • (1995) Br J Haematol , vol.89 , pp. 868-873
    • Giardini, C.1    Galimberti, M.2    Lucarelli, G.3
  • 24
    • 0037035540 scopus 로고    scopus 로고
    • Reversibility of cirrhosis in patients cured of thalassemia by bone marrow transplantation
    • Muretto P, Angelucci E, Lucarelli G: Reversibility of cirrhosis in patients cured of thalassemia by bone marrow transplantation. Ann Intern Med 2002, 136:667-672. • This is the first observation of reversibility of cirrhosis following iron depletion in patients who underwent BMT for thalassemia.
    • (2002) Ann Intern Med , vol.136 , pp. 667-672
    • Muretto, P.1    Angelucci, E.2    Lucarelli, G.3
  • 25
    • 0027166344 scopus 로고
    • Growth in children after bone marrow transplantation for thalassemia
    • Gaziev D, Galimberti M, Giardini C, et al.: Growth in children after bone marrow transplantation for thalassemia. Bone Marrow Transplant 1993, 12(suppl 1):100-101.
    • (1993) Bone Marrow Transplant , vol.12 , Issue.SUPPL. 1 , pp. 100-101
    • Gaziev, D.1    Galimberti, M.2    Giardini, C.3
  • 26
    • 0034903639 scopus 로고    scopus 로고
    • Final height of thalassemic patients who underwent bone marrow transplantation during childhood
    • De Simone M, Verrotti A, Iughetti L, et al.: Final height of thalassemic patients who underwent bone marrow transplantation during childhood. Bone Marrow Transplant 2001, 28:201-205.
    • (2001) Bone Marrow Transplant , vol.28 , pp. 201-205
    • De Simone, M.1    Verrotti, A.2    Iughetti, L.3
  • 27
    • 0030895905 scopus 로고    scopus 로고
    • Growth and development in ex-thalassemic patients
    • De Sanctis V, Galimberti M, Lucarelli G, et al.: Growth and development in ex-thalassemic patients. Bone Marrow Transplant 1997, 19(suppl 2):126-127.
    • (1997) Bone Marrow Transplant , vol.19 , Issue.SUPPL. 2 , pp. 126-127
    • De Sanctis, V.1    Galimberti, M.2    Lucarelli, G.3
  • 28
    • 0030968020 scopus 로고    scopus 로고
    • Graft-versus-host disease after bone marrow transplantation for thalassemia: An analysis of incidence and risk factors
    • Gaziev D, Polchi P, Galimberti M, et al.: Graft-versus-host disease after bone marrow transplantation for thalassemia: an analysis of incidence and risk factors. Transplantation 1997, 63:854-860.
    • (1997) Transplantation , vol.63 , pp. 854-860
    • Gaziev, D.1    Polchi, P.2    Galimberti, M.3
  • 29
    • 0030904390 scopus 로고    scopus 로고
    • Malignancies after bone marrow transplantation for thalassemia
    • Gaziev D, Lucarelli G, Galimberti M, et al.: Malignancies after bone marrow transplantation for thalassemia. Bone Marrow Transplant 1997, 19(suppl 2):142-144.
    • (1997) Bone Marrow Transplant , vol.19 , Issue.SUPPL. 2 , pp. 142-144
    • Gaziev, D.1    Lucarelli, G.2    Galimberti, M.3
  • 30
    • 0028291736 scopus 로고
    • Mortality in sickle cell disease: Life expectancy and risk factors for early death
    • Platt OS, Brambilla DJ, Rosse WF, et al.: Mortality in sickle cell disease: life expectancy and risk factors for early death. N Engl J Med 1994, 330:1639-1644.
    • (1994) N Engl J Med , vol.330 , pp. 1639-1644
    • Platt, O.S.1    Brambilla, D.J.2    Rosse, W.F.3
  • 31
    • 0029257849 scopus 로고
    • Natural history and determinants of clinical severity of sickle cell disease
    • Serjeant GR. Natural history and determinants of clinical severity of sickle cell disease. Curr Opin Hematol 1995, 2:103-108.
    • (1995) Curr Opin Hematol , vol.2 , pp. 103-108
    • Serjeant, G.R.1
  • 32
    • 0021593369 scopus 로고
    • Bone marrow transplantation in a patient with sickle cell anemia
    • Jonson FL, Look AT, Gockerman J, et al.: Bone marrow transplantation in a patient with sickle cell anemia. N Engl J Med 1984, 311:780-783.
    • (1984) N Engl J Med , vol.311 , pp. 780-783
    • Jonson, F.L.1    Look, A.T.2    Gockerman, J.3
  • 35
    • 0031870487 scopus 로고    scopus 로고
    • Haematopoietic stem cell transplantation for sickle cell anaemia: The first 50 patients transplanted in Belgium
    • Vermylen C, Cornu G, Ferster A, et al.: Haematopoietic stem cell transplantation for sickle cell anaemia: the first 50 patients transplanted in Belgium. Bone Marrow Transplant 1998, 22:1-6.
    • (1998) Bone Marrow Transplant , vol.22 , pp. 1-6
    • Vermylen, C.1    Cornu, G.2    Ferster, A.3
  • 36
    • 0030905444 scopus 로고    scopus 로고
    • Bone marrow transplantation in sickle cell disorders in Pesaro
    • Giardini C, Galimberti M, Lucarelli G, et al.: Bone marrow transplantation in sickle cell disorders in Pesaro. Bone Marrow Transplant 1997, 19(suppl 2):106-109.
    • (1997) Bone Marrow Transplant , vol.19 , Issue.SUPPL. 2 , pp. 106-109
    • Giardini, C.1    Galimberti, M.2    Lucarelli, G.3
  • 37
    • 0030959935 scopus 로고    scopus 로고
    • Report of the French experience concerning 26 children transplanted for severe sickle cell disease
    • Bernaudin F, Souillet G, Vannier JP, et al.: Report of the French experience concerning 26 children transplanted for severe sickle cell disease. Bone Marrow Transplant 1997, 19(suppl 2):112-115.
    • (1997) Bone Marrow Transplant , vol.19 , Issue.SUPPL. 2 , pp. 112-115
    • Bernaudin, F.1    Souillet, G.2    Vannier, J.P.3
  • 38
    • 0034654139 scopus 로고    scopus 로고
    • Impact of bone marrow transplantation for symptomatic sickle cell disease: An interim report
    • Walters MC, Storb R, Patience M, et al.: Impact of bone marrow transplantation for symptomatic sickle cell disease: an interim report. Blood 2000, 95:1918-1924.
    • (2000) Blood , vol.95 , pp. 1918-1924
    • Walters, M.C.1    Storb, R.2    Patience, M.3
  • 39
    • 0028966027 scopus 로고
    • Neurologic complications after allogeneic marrow transplantation
    • Walters MC, Sullivan KM, Bernaudin F, et al.: Neurologic complications after allogeneic marrow transplantation. Blood 1995, 85:879-884.
    • (1995) Blood , vol.85 , pp. 879-884
    • Walters, M.C.1    Sullivan, K.M.2    Bernaudin, F.3
  • 40
    • 0034928876 scopus 로고    scopus 로고
    • Analysis of chimerism in thalassemic children undergoing stem cell transplantation
    • Amrolia PJ, Vulliamy T, Vassiliou G, et al.: Analysis of chimerism in thalassemic children undergoing stem cell transplantation. Br J Haematol 2001, 114:219-225.
    • (2001) Br J Haematol , vol.114 , pp. 219-225
    • Amrolia, P.J.1    Vulliamy, T.2    Vassiliou, G.3
  • 41
    • 0035544031 scopus 로고    scopus 로고
    • Stable mixed hematopoietic chimerism after bone marrow transplantation for sickle cell anemia
    • Walters MC, Patience M, Leisenring W, et al.: Stable mixed hematopoietic chimerism after bone marrow transplantation for sickle cell anemia. Biol Blood Marrow Transplant 2001, 7:665-673. • This report is the largest published to date on stable mixed chimerism after conventional myeloablative transplantation for sickle cell anemia. The study shows that the incidence of stable mixed chimerism after BMT for sickle cell disease is 26%, and some patients with HbAA donors had mixed chimerism levels of 11%, 67%, and 74%, whereas the levels of HbS on electrophoresis were 7%, 0%, and 0%, respectively, probably as a result of donor erythroid progenitors and/or erythrocytes advantage over sickle cell counterparts.
    • (2001) Biol Blood Marrow Transplant , vol.7 , pp. 665-673
    • Walters, M.C.1    Patience, M.2    Leisenring, W.3
  • 42
    • 0036209012 scopus 로고    scopus 로고
    • Re: Measurement of chimerism after hematopoietic stem cell transplantation
    • Woodard P, Cunningham JM: Re: measurement of chimerism after hematopoietic stem cell transplantation [letter]. Biol Blood Marrow Transplant 2002, 8:170.
    • (2002) Biol Blood Marrow Transplant , vol.8 , pp. 170
    • Woodard, P.1    Cunningham, J.M.2
  • 43
    • 0036190198 scopus 로고    scopus 로고
    • Novel conditioning regimens and nonmyeloablative stem cell transplants
    • Baker SK, Wagner JE: Novel conditioning regimens and nonmyeloablative stem cell transplants. Curr Opin Pediatr 2002, 1:17-22. • This is a more recent review on novel nonmyeloablative or less intensive conditioning regimens for stem cell transplantation in malignant and nonmalignant hematological diseases.
    • (2002) Curr Opin Pediatr , vol.1 , pp. 17-22
    • Baker, S.K.1    Wagner, J.E.2
  • 44
    • 0032006125 scopus 로고    scopus 로고
    • Nonmyeloablative stem cell transplantation and cell therapy as an alternative to conventional bone marrow transplantation with lethal cytoreduction for the treatment of malignant and nonmalignant hematologic diseases
    • Slavin S, Nagler A, Naparstek E, et al.: Nonmyeloablative stem cell transplantation and cell therapy as an alternative to conventional bone marrow transplantation with lethal cytoreduction for the treatment of malignant and nonmalignant hematologic diseases. Blood 1998, 91:756-763.
    • (1998) Blood , vol.91 , pp. 756-763
    • Slavin, S.1    Nagler, A.2    Naparstek, E.3


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.