메뉴 건너뛰기




Volumn 7, Issue 9, 1996, Pages 1123-1129

Molecular analysis of T lymphocyte-directed gene therapy for adenosine deaminase deficiency: Long-term expression in vivo of genes introduced with a retroviral vector

Author keywords

[No Author keywords available]

Indexed keywords

ADENOSINE DEAMINASE; COMPLEMENTARY DNA; MESSENGER RNA; PHOSPHOTRANSFERASE;

EID: 0029945161     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.1996.7.9-1123     Document Type: Article
Times cited : (42)

References (32)
  • 1
    • 0024997299 scopus 로고
    • Paradoxical expression of adenosine deaminase in T cells cultured from a patient with adenosine deaminase deficiency and combined immunodeficiency
    • ARREDONDO-VEGA, F.X., KURTZBERG, J., CHAFFEE, S., SANTISTEBAN, I., REISNER, E., POVEY, M.S., and HERSHFIELD, M.S. (1990). Paradoxical expression of adenosine deaminase in T cells cultured from a patient with adenosine deaminase deficiency and combined immunodeficiency. J. Clin. Invest. 86, 444-452.
    • (1990) J. Clin. Invest. , vol.86 , pp. 444-452
    • Arredondo-Vega, F.X.1    Kurtzberg, J.2    Chaffee, S.3    Santisteban, I.4    Reisner, E.5    Povey, M.S.6    Hershfield, M.S.7
  • 4
    • 0024401665 scopus 로고
    • Retroviral vector-mediated high-efficiency expression of adenosine deaminase (ADA) in hematopoietic long-term cultures of ADA-deficient marrow cells
    • BORDIGNON, C., YU, S.F., SMITH, C.A., HANTZOPOULOS, P., UNGERS, G.E., KEEVER, C.A., O'REILLY, R.J., and GILBOA, E. (1989). Retroviral vector-mediated high-efficiency expression of adenosine deaminase (ADA) in hematopoietic long-term cultures of ADA-deficient marrow cells. Proc. Natl. Acad. Sci. USA 86, 6748-6752.
    • (1989) Proc. Natl. Acad. Sci. USA , vol.86 , pp. 6748-6752
    • Bordignon, C.1    Yu, S.F.2    Smith, C.A.3    Hantzopoulos, P.4    Ungers, G.E.5    Keever, C.A.6    O'Reilly, R.J.7    Gilboa, E.8
  • 5
    • 0026573186 scopus 로고
    • Genetic correction of cultured T cells from an adenosine deaminase-deficient patient: Characteristics of non-transduced and transduced T cells
    • BRAAKMAN, E., VAN BEUSECHEM, V.W., VAN KRIMPEN, B.A., FISCHER, A., BOLHUIS, R.L., and VALERIO, D. (1992). Genetic correction of cultured T cells from an adenosine deaminase-deficient patient: characteristics of non-transduced and transduced T cells. Eur. J. Immunol. 22, 63-69.
    • (1992) Eur. J. Immunol. , vol.22 , pp. 63-69
    • Braakman, E.1    Van Beusechem, V.W.2    Van Krimpen, B.A.3    Fischer, A.4    Bolhuis, R.L.5    Valerio, D.6
  • 9
    • 0019462298 scopus 로고
    • Characteristics of an aminohydrolase distinct from adenosine deaminase in cultured human lymphoblasts
    • DADDONA, P.E., and KELLEY, W.N. (1981). Characteristics of an aminohydrolase distinct from adenosine deaminase in cultured human lymphoblasts. Biochem. Biophys. Acta 658, 280-290.
    • (1981) Biochem. Biophys. Acta , vol.658 , pp. 280-290
    • Daddona, P.E.1    Kelley, W.N.2
  • 12
    • 0026670175 scopus 로고
    • Transfer of the ADA gene into human ADA-deficient T lymphocytes reconstitutes specific immune functions
    • FERRARI, G., ROSSINI, S., NOBILI, N., MAGGIONI, D., GAROFALO, A., GIAVAZZI, R., MAVILIO, F., and BORDIGNON, C. (1992). Transfer of the ADA gene into human ADA-deficient T lymphocytes reconstitutes specific immune functions. Blood 80, 1120-1124.
    • (1992) Blood , vol.80 , pp. 1120-1124
    • Ferrari, G.1    Rossini, S.2    Nobili, N.3    Maggioni, D.4    Garofalo, A.5    Giavazzi, R.6    Mavilio, F.7    Bordignon, C.8
  • 13
    • 0027469895 scopus 로고
    • Enzyme replacement therapy with polyethylene glycol-adenosine deaminase in adenosine deaminase deficiency: Overview and case reports of three patients, including two now receiving gene therapy
    • HERSHRELD, M.S., CHAFFEE, S., and SORENSEN, R.U. (1993). Enzyme replacement therapy with polyethylene glycol-adenosine deaminase in adenosine deaminase deficiency: overview and case reports of three patients, including two now receiving gene therapy. Pediatr. Res. 33, S42-7.
    • (1993) Pediatr. Res. , vol.33
    • Hershreld, M.S.1    Chaffee, S.2    Sorensen, R.U.3
  • 14
    • 0025690483 scopus 로고
    • Adenosine deaminase deficiency
    • HIRSCHHORN, R. (1990). Adenosine deaminase deficiency. Immunodefic. Rev. 2, 175-198.
    • (1990) Immunodefic. Rev. , vol.2 , pp. 175-198
    • Hirschhorn, R.1
  • 15
    • 0026009087 scopus 로고
    • Homozygosity for a newly identified missense mutation in a patient with very severe combined immunodeficiency due to adenosine deaminase deficiency (ADA-SCID)
    • HIRSCHHORN, R., CHAKRAVARTI, V., PUCK, J., and DOUGLAS, S.D. (1991). Homozygosity for a newly identified missense mutation in a patient with very severe combined immunodeficiency due to adenosine deaminase deficiency (ADA-SCID). Am. J. Hum. Genet. 49, 878-885.
    • (1991) Am. J. Hum. Genet. , vol.49 , pp. 878-885
    • Hirschhorn, R.1    Chakravarti, V.2    Puck, J.3    Douglas, S.D.4
  • 16
    • 0024392134 scopus 로고
    • Expression of human adenosine deamianse from various strong promoters after gene transfer into human hematopoietic cell lines
    • HOCK, R.A., MILLER, A.D., and OSBORNE, W.R. (1989). Expression of human adenosine deamianse from various strong promoters after gene transfer into human hematopoietic cell lines. Blood 74, 876-881.
    • (1989) Blood , vol.74 , pp. 876-881
    • Hock, R.A.1    Miller, A.D.2    Osborne, W.R.3
  • 20
    • 0022767368 scopus 로고
    • Redesign of retrovirus packaging cell lines to avoid recombination leading to helper virus production
    • MILLER, A.D., and BUTTIMORE, C. (1987). Redesign of retrovirus packaging cell lines to avoid recombination leading to helper virus production. Mol. Cell. Biol. 6, 2895-2902.
    • (1987) Mol. Cell. Biol. , vol.6 , pp. 2895-2902
    • Miller, A.D.1    Buttimore, C.2
  • 21
    • 0027248755 scopus 로고
    • Human cord blood cells as targets for gene transfer potential use in genetic therapies of severe combined immunodeficiency disease
    • MORITZ, T., KELLER, D.C., and WILLIAMS, D.A. (1993). Human cord blood cells as targets for gene transfer potential use in genetic therapies of severe combined immunodeficiency disease. J. Exp. Med. 178, 529-536.
    • (1993) J. Exp. Med. , vol.178 , pp. 529-536
    • Moritz, T.1    Keller, D.C.2    Williams, D.A.3
  • 22
    • 0343678858 scopus 로고
    • Generation and maintenance of T cell lines and clones
    • J.E. Coligan, A.M. Kruisbeek, D.H. Margulies, E.M. Shevach, and W. Strober, eds. (John Wiley and Sons, New York)
    • NUTMAN, T.B. (1991). Generation and maintenance of T cell lines and clones. In Current Protocols in Immunology. J.E. Coligan, A.M. Kruisbeek, D.H. Margulies, E.M. Shevach, and W. Strober, eds. (John Wiley and Sons, New York) pp. 7.19-7.19.7.
    • (1991) Current Protocols in Immunology
    • Nutman, T.B.1
  • 23
    • 0023101785 scopus 로고
    • Efficient retrovirus-mediated transfer and expression of a human adenosine deaminase gene in diploid skin fibrobasts from an adenosine deaminase-deficient human
    • PALMER, T.D., HOCK, R.A., OSBORNE, W.R., and MILLER, A.D. (1987). Efficient retrovirus-mediated transfer and expression of a human adenosine deaminase gene in diploid skin fibrobasts from an adenosine deaminase-deficient human. Proc. Natl. Acad. Sci. USA 84, 1055-1059.
    • (1987) Proc. Natl. Acad. Sci. USA , vol.84 , pp. 1055-1059
    • Palmer, T.D.1    Hock, R.A.2    Osborne, W.R.3    Miller, A.D.4
  • 24
    • 0025976935 scopus 로고
    • Genetically modified skin fibroblasts persist long after transplantation but gradually inactivate introduced genes
    • PALMER, T.D., ROSMAN, G.J., OSBORNE, W.R., and MILLER, A.D. (1991). Genetically modified skin fibroblasts persist long after transplantation but gradually inactivate introduced genes. Proc. Natl. Acad. Sci. USA 88, 1330-1334.
    • (1991) Proc. Natl. Acad. Sci. USA , vol.88 , pp. 1330-1334
    • Palmer, T.D.1    Rosman, G.J.2    Osborne, W.R.3    Miller, A.D.4
  • 25
    • 0019466071 scopus 로고
    • Serum adenosine deaminase in normals and in a patient with adenosine deaminase deficient-severe combined immunodeficiency
    • RATECH, H., and HIRSCHHORN, R. (1981). Serum adenosine deaminase in normals and in a patient with adenosine deaminase deficient-severe combined immunodeficiency. Clinica Chimica Acta 115, 341-347.
    • (1981) Clinica Chimica Acta , vol.115 , pp. 341-347
    • Ratech, H.1    Hirschhorn, R.2
  • 26
    • 0021685423 scopus 로고
    • A new sensitive method for qualitative and quantitative assay of neomycin phosphotransferase in crude cell extracts
    • REISS, B., SPRENGEL, R., WILL, H., and SCHALLER, H. (1984). A new sensitive method for qualitative and quantitative assay of neomycin phosphotransferase in crude cell extracts. Gene 30, 211-217.
    • (1984) Gene , vol.30 , pp. 211-217
    • Reiss, B.1    Sprengel, R.2    Will, H.3    Schaller, H.4
  • 28
    • 0018187599 scopus 로고
    • Characterization of the residual adenosine deaminating activity in the spleen of a patient with combined immunodeficiency disease and adenosine deaminase deficiency
    • SCHRADER, W.P., POLLARA, B., and MEUWISSEN, H. (1978). Characterization of the residual adenosine deaminating activity in the spleen of a patient with combined immunodeficiency disease and adenosine deaminase deficiency. Proc. Natl. Acad. Sci. USA 75, 446-450.
    • (1978) Proc. Natl. Acad. Sci. USA , vol.75 , pp. 446-450
    • Schrader, W.P.1    Pollara, B.2    Meuwissen, H.3
  • 30
    • 0026666055 scopus 로고
    • Long-term expression of human adenosine deaminase in rhesus monkeys transplanted with retrovirus-infected bone-marrow cells
    • VAN BEUSECHEM, V.W., KUKLER, A., HEIDT, PJ., and VALERIO, D. (1992). Long-term expression of human adenosine deaminase in rhesus monkeys transplanted with retrovirus-infected bone-marrow cells. Proc. Natl. Acad. Sci. USA 89, 7640-7644.
    • (1992) Proc. Natl. Acad. Sci. USA , vol.89 , pp. 7640-7644
    • Van Beusechem, V.W.1    Kukler, A.2    Heidt, P.J.3    Valerio, D.4
  • 31
    • 0021760867 scopus 로고
    • Sequence of human adenosine deaminase cDNA including the coding region and a small intron
    • WIGINTON, D.A., ADRIAN, G.S., and HUTTON, J.J. (1984). Sequence of human adenosine deaminase cDNA including the coding region and a small intron. Nucleic Acids. Res. 12, 2439-2446.
    • (1984) Nucleic Acids. Res. , vol.12 , pp. 2439-2446
    • Wiginton, D.A.1    Adrian, G.S.2    Hutton, J.J.3
  • 32
    • 0022552808 scopus 로고
    • Retrovirus-mediated transfer of human adenosine deaminase gene sequences into cells in culture and into murine hematopoietic cells in vivo
    • WILLIAMS, D.A., ORKIN, S.H., and MULLIGAN, R.C. (1986). Retrovirus-mediated transfer of human adenosine deaminase gene sequences into cells in culture and into murine hematopoietic cells in vivo. Proc. Natl. Acad. Sci. USA 83, 2566-2570.
    • (1986) Proc. Natl. Acad. Sci. USA , vol.83 , pp. 2566-2570
    • Williams, D.A.1    Orkin, S.H.2    Mulligan, R.C.3


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.