Enhanced survival in Sandhoff disease mice receiving a combination of substrate deprivation therapy and bone marrow transplantation

Blood

Volumn 97, Issue 1, 2001, Pages 327-329

  Jeyakumar, Mylvaganam ^c   Norflus, Francine ^c   Tiff, Cynthia J ^c   Cortina Borja, Mario ^c   Butters, Terry D ^c   Proia, Richard L ^c   Perry, V Hugh ^c   Dwek, Raymond A ^c   Platt, Frances M ^a,b  

^a Lister Institute of Preventive Medicine   (United Kingdom)

^b UNIVERSITY OF OXFORD   (United Kingdom)

^c NONE

Author keywords

[No Author keywords available]

Indexed keywords

BETA N ACETYLHEXOSAMINIDASE; GANGLIOSIDE GM2; GLYCOSPHINGOLIPID;

ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; BONE MARROW TRANSPLANTATION; CHEMICAL ANALYSIS; ENZYME ACTIVITY; LIPOGENESIS; LYSOSOME STORAGE DISEASE; MOUSE; NONHUMAN; PRIORITY JOURNAL; SANDHOFF DISEASE; STATISTICAL ANALYSIS;

EID: 0035168688     PISSN: 00064971     EISSN: None     Source Type: Journal    
DOI: 10.1182/blood.V97.1.327     Document Type: Article

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