Prospects for prenatal gene therapy in disorders causing mental retardation

Mental Retardation and Developmental Disabilities Research Reviews

Volumn 7, Issue 1, 2001, Pages 65-72

  Ye, Xuehai ^a   Mitchell, Melanie ^a   Newman, Kurt ^a   Batshaw, Mark L ^a  

^a GEORGE WASHINGTON UNIVERSITY SCHOOL OF MEDICINE AND HEALTH SCIENCES   (United States)

Author keywords

Bioethics; Genetic diseases; In utero gene transfer; Prenatal gene therapy

Indexed keywords

ALPHA GLOBIN; BETA N ACETYLHEXOSAMINIDASE; CEREBROSIDE SULFATASE; DNA; DYSTROPHIN; FUMARYLACETOACETASE; GLUCAN 1,4 ALPHA GLUCOSIDASE; GLUCOSYLCERAMIDASE; GLUCURONOSYLTRANSFERASE; HEMOGLOBIN; IDURONATE 2 SULFATASE; KALININ; LEVO IDURONIDASE; LIPOSOME; NEUROTROPHIN 3; ORNITHINE CARBAMOYLTRANSFERASE; TRANSMEMBRANE CONDUCTANCE REGULATOR; VIRUS VECTOR;

CARCINOGENESIS; DELIVERY; DNA VECTOR; DRUG INDUCED DISEASE; DRUG SAFETY; DRUG TOLERANCE; ETHICS; FETUS DEVELOPMENT; GENE EXPRESSION; GENE THERAPY; GENE TRANSFER; GENETIC DISORDER; GERM LINE; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; LUNG ALVEOLUS EPITHELIUM; MENTAL DEFICIENCY; MUTAGENESIS; NONHUMAN; PATHOGENESIS; PLACENTA; PRENATAL PERIOD; PRIORITY JOURNAL; REVIEW; TARGET CELL;

ANIMALS; ETHICS, MEDICAL; FEMALE; GENE THERAPY; GENE TRANSFER TECHNIQUES; HUMANS; INFANT, NEWBORN; MENTAL RETARDATION; MICE; OUTCOME AND PROCESS ASSESSMENT (HEALTH CARE); PREGNANCY; PRENATAL CARE; RISK FACTORS;

EID: 0035106067     PISSN: 10804013     EISSN: None     Source Type: Journal    
DOI: 10.1002/1098-2779(200102)7:1<65::AID-MRDD1009>3.0.CO;2-9     Document Type: Review

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