Stem-cell transplantation for inherited immunodeficiency disorders

Pediatric Clinics of North America

Volumn 47, Issue 6, 2000, Pages 1371-1387

  Horwitz, Mitchell E ^b  

^a NATIONAL INSTITUTE OF ALLERGY AND INFECTIOUS DISEASES   (United States)

^b NONE

Author keywords

[No Author keywords available]

Indexed keywords

HLA ANTIGEN; MYELOABLATIVE AGENT;

ALLOTRANSPLANTATION; AUTOTRANSPLANTATION; CHEDIAK HIGASHI SYNDROME; CHRONIC GRANULOMATOUS DISEASE; COMBINED IMMUNODEFICIENCY; HEMOPHAGOCYTIC SYNDROME; HLA MATCHING; HUMAN; IMMUNE DEFICIENCY; LEUKOCYTE ADHESION DEFICIENCY; REVIEW; STEM CELL TRANSPLANTATION; WISKOTT ALDRICH SYNDROME;

EID: 0034529419     PISSN: 00313955     EISSN: None     Source Type: Journal    
DOI: 10.1016/S0031-3955(05)70276-5     Document Type: Article

References (92)

1. Successful bone marrow transplantation from an HLA-identical unrelated donor in a patient with hemophagocytic lymphohistiocytosis
2. Bone marrow transplantation in a patient with the Wiskott-Aldrich Syndrome
3. Successful correction of hemophagocytic lymphohistiocytosis with related or unrelated bone marrow transplantation
4. The accelerated phase of Chediak-Higashi syndrome
5. Bone marrow transplantation in cartilage-hair hypoplasia: Correction of the immunodeficiency but not of the chondrodysplasia
6. Allogeneic bone marrow transplantation for hemophagocytic lymphohistiocytosis in Sweden
7. Bone marrow transplantation as treatment for X-linked immunodeficiency with hyper-IgM
8. Marrow transplantation from human leukocyte antigen-identical or haploidentical donors for correction of Wiskott-Aldrich syndrome
9. Correction of purine nucleoside phosphorylase deficiency by transplantation of allogeneic bone marrow from a sibling
10. Predictive factors for acute graft-versus-host disease in patients transplanted with HLA-identical bone marrow
11. Development of immunity in human severe primary T cell deficiency following haploidentical bone marrow stem cell transplantation
12. Hematopoietic stem-cell transplantation for the treatment of severe combined immunodeficiency
13. Haploidentical bone marrow stem cell transplantation in human severe combined immunodeficiency
14. Bone marrow transplantation for primary immunodeficiency diseases
15. Marrow transplantation from HLA non-identical family donors for the treatment of leukemia: A pilot study of 15 patients using additional immunosuppression and T-cell depletion
16. Bone marrow transplantation in chronic granulomatous disease
17. Late diagnosis and correction of purine nucleoside phosphorylase deficiency with allogeneic bone marrow transplantation
18. Engraftment kinetics after nonmyeloablative allogeneic peripheral blood stem cell transplantation: Full donor T-cell chimerism precedes alloimmune responses
19. Reduced toxicity and transplant related mortality following nonmyeloablative allogeneic peripheral blood stem cell transplantation for malignant disease
20. Identification of a graft versus host disease-associated human minor histocompatibility antigen
21. Reconstitution of normal neutrophil function in chronic granulomatous disease by bone marrow transplantation
22. Improved outcome in haemophagocytic lymphohistiocytosis after bone marrow transplantation from related and unrelated donors: A single-centre experience of 12 patients
23. Graft versus leukemia effect in man: The relapse rate of acute leukemia is lower after allogeneic than after syngeneic marrow transplantation
24. Unrelated donor bone marrow transplantation for correction of lethal congenital immunodeficiencies
25. Graft-versus-host disease prevention in allogeneic bone marrow transplantation from histocompatible siblings: A pilot study using immunotoxins for T cell depletion of donor bone marrow
26. Bone-marrow transplantation for immunodeficiencies and osteopetrosis: European survey, 1968-1985
27. European experience of bone-marrow transplantation for severe combined immunodeficiency
28. Treatment of X-linked severe combined immunodeficiency by in utero transplantation of paternal bone marrow
29. Previous donor pregnancy as a risk factor for acute graft-versus-host disease in patients with aplastic anaemia treated by allogeneic marrow transplantation
30. Bone marrow transplantation in immunodeficiency diseases
31. Immunological reconstitution of sex-linked lymphopenic immunological deficiency
32. Allogeneic bone marrow transplantation: The monitoring of granulocyte macrophage colonies following the collection of bone marrow mononuclear cells and after the subsequent in-vitro cytolysis of OKT3 positive lymphocytes
33. Bone marrow transplantation: Correction of immune deficit in lymphopenic immunologic deficiency and correction of an immunologically induced pancytopenia
34. Mismatches of minor histocompatibility antigens between HLA-identical donors and recipients and the development of graft-versushost disease after bone marrow transplantation
35. A syndrome associating partial albinism and immunodeficiency
36. Long-term chimerism and B-cell function after bone marrow transplantation in patients with severe combined immunodeficiency with B cells: A single-center study of 22 patients
37. Treatment of Chediak-Higashi syndrome by allogenic bone marrow transplantation: Report of 10 cases
38. Correction of the hyper-IgM syndrome after liver and bone marrow transplantation
39. Treatment of adenosine deaminase deficiency with polyethylene glycol-modified adenosine deaminase
40. Removal of marrow T cells with OKT3-OKT11 monoclonal antibodies and complement to prevent acute graft-versus-host disease: A pilot study in ten patients
41. Successful bone marrow transplantation in a child with X-linked chronic granulomatous disease
42. Associations of the skeletal and immune systems
43. Nonmyeloablative, T-cell depleted allogeneic peripheral blood stem cell transplantation for patients with chronic granulomatous disease
44. Treatment of familial hemophagocytic lymphohistiocytosis with bone marrow transplantation from HLA genetically nonidentical donors
45. Marrow transplantation in chronic granulomatous disease: An update, with 6-year follow-up
46. Bone marrow transplantation in chronic granulomatous disease
47. Successful bone marrow transplantation in a child with X-linked hyper-IgM syndrome
48. Immunological reconstitution by allogenic bone marrow transplantation in a child with the X-linked hyper-IgM syndrome
49. Bone marrow transplantation for severe combined immunodeficiency disease: Reported from 1968 to 1977
50. Transplant-lite: Induction of graft-versus-malignancy using fludarabine-based nonablative chemotherapy and allogeneic blood progenitor-cell transplantation as treatment for lymphoid malignancies
51. Bone marrow transplantation in major histocompatibility complex class II deficiency: A single-center study of 19 patients
52. Partial albinism with immunodeficiency (Griscelli syndrome)
53. Cartilage hair hypoplasia in infancy: A misleading chondrodysplasia
54. Attempted bone-marrow transplantation in a 17-week fetus
55. Matched unrelated donor bone marrow transplantation in leukocyte adhesion deficiency
56. Selective depletion of marrow-T cytotoxic lymphocytes (CD8) in the prevention of graft-versus-host disease after allogeneic bone-marrow transplantation
57. Effects of in vitro depletion of T cells in HLA-identical allogeneic marrow grafts
58. Effects of treating marrow with a CD3-specific immunotoxin for prevention of acute graft-versus-host disease
59. Treatment of donor bone marrow with monoclonal anti-T-cell antibody and complement for the prevention of graft-versus-host disease: A prospective, randomized, double-blind trial
60. Degree of early donor T-cell chimerism predicts GVHD and graft rejection in patients with nonmyeloablative hematopoietic stem cell allografts
61. Donor lymphocyte infusion postnon-myeloablative allogeneic peripheral blood stem cell transplantation for chronic granulomatous disease
62. Marrow transplantation for congenital disorders
63. Transplantation of hematopoietic cells for lethal congenital immunodeficiencies
64. The use of HLA-non-identical T-cell-depleted marrow transplants for correction of severe combined immunodeficiency disease
65. Bone marrow transplantation in 26 patients with Wiskott-Aldrich syndrome from a single center
66. Successful treatment of invasive aspergillosis in chronic granulomatous disease by bone marrow transplantation, granulocyte colony-stimulating factor-mobilized granulocytes, and liposomal amphotericin-B
67. Complete correction of the Wiskott-Aldrich Syndrome by allogeneic bone marrow transplantation
68. Lymphohematopoietic graft-vs.-host reactions can be induced without graft-vs.-host disease in murine mixed chimeras established with a cyclophosphamide-based nonmyeloablative conditioning regimen
69. Impaired natural killer activity in lymphohistiocytosis syndrome
70. Depletion of T lymphocytes in donor marrow prevents significant graft-versus-host disease in matched allogeneic leukaemic marrow transplant recipients
71. Allogeneic bone marrow transplantation for chronic granulomatous disease
72. Reconstitution after transplantation with T-lymphocyte-depleted HLA haplotype-mismatched bone marrow for severe combined immunodeficiency
73. Transplantation for severe combined immunodeficiency with HLA-A,B,D,DR incompatible parental marrow cells fractionated by soybean agglutinin and sheep red blood cells
74. Bone marrow transplantation (BMT) for the syndrome of pigmentary dilution and lymphohistiocytosis (Griscelli's syndrome)
75. Correction of neutropenia and hypogammaglobulinemia in X-linked hyper-IgM syndrome by allogeneic bone marrow transplantation
76. Nonmyeloablative stem cell transplantation and cell therapy as an alternative to conventional bone marrow transplantation with lethal cytoreduction for the treatment of malignant and nonmalignant hematologic diseases
77. Clinical application of intrauterine bone marrow transplantation for treatment of genetic diseases: Feasibility studies
78. Successful HLA-identical sibling cord blood transplantation in a 6-year-old boy with leukocyte adhesion deficiency syndrome
79. Histiocytoses
80. Severe combined immunodeficiency: A retrospective single-center study of clinical presentation and outcome in 117 patients
81. Intrauterine bone-marrow transplantation at 12 weeks' gestation
82. Brief report: Correction of X-linked hyper-IgM syndrome by allogeneic bone marrow transplantation
83. Results of allogeneic bone marrow transplantation in patients with leukocyte adhesion deficiency
84. One hundred patients with acute leukemia treated by chemotherapy, total body irradiation, and allogeneic marrow transplantation
85. Treatment of human fetuses and induction of immunological tolerance in humans by in utero transplantation of stem cells into fetal recipients
86. In-utero transplantation of stem cells in bare lymphocyte syndrome
87. Clinical trial depleting T lymphocytes from donor marrow for matched and mismatched allogeneic bone marrow transplants
88. Reversal of natural killer defect in a patient with Chediak-Higashi syndrome after bone-marrow transplantation
89. Elimination of graft-versus-host disease by in-vitro depletion of alloreactive lymphocytes with a monoclonal rat anti-human lymphocyte antibody (CAMPATH-1)
90. Antileukemic effect of graft-versus-host disease in human recipients of allogeneic-marrow grafts
91. Risk factors for acute graft-versus-host disease in histocompatible donor bone marrow transplantation
92. In-utero transplantation of parental CD34 haematopoietic progenitor cells in a patient with X-linked severe combined immuno-deficiency (SCIDXI)