Gaucher disease;La maladie de Gaucher

Hematologie

Volumn 5, Issue 6, 1999, Pages 480-493

  Germain, Dominique P ^a  

^a HÔPITAL BROUSSAIS   (France)

Author keywords

Enzyme replacement therapy; Gaucher's disease; Gene therapy; Lysosomal storage disorders; Mutations; Orphan diseases

Indexed keywords

ALGLUCERASE; GLUCOSYLCERAMIDASE; IMIGLUCERASE;

CLINICAL FEATURE; DISEASE CLASSIFICATION; ENZYME DEFICIENCY; ENZYME REPLACEMENT; GAUCHER DISEASE; GENE MUTATION; GENE THERAPY; HUMAN; JEW; REVIEW;

EID: 0033386675     PISSN: 12647527     EISSN: None     Source Type: Journal    
DOI: None     Document Type: Review

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