Human gene therapy for hereditary diseases: A review of trials

American Journal of Health-System Pharmacy

Volumn 55, Issue 9, 1998, Pages 899-904

  Knoell, Daren L ^a   Yiu, Irene M ^a  

^a OHIO STATE UNIVERSITY   (United States)

Author keywords

Clinical studies; Cystic fibrosis; Drug administration; Gene therapy; Genetics; Hereditary diseases; Hypercholesterolemia; Toxicity

Indexed keywords

ADENOSINE DEAMINASE;

CYSTIC FIBROSIS; ENZYME DEFICIENCY; FAMILIAL HYPERCHOLESTEROLEMIA; GENE EXPRESSION; GENE TARGETING; GENE THERAPY; GENE TRANSFER; GENETIC DISORDER; HUMAN; PRIORITY JOURNAL; RECOMBINANT GENE; REVIEW; TRANSGENE;

EID: 0032080721     PISSN: 10792082     EISSN: None     Source Type: Journal    
DOI: 10.1093/ajhp/55.9.899     Document Type: Review

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