Development of safe and efficient retroviral vectors for Gaucher disease

Gene Therapy

Volumn 4, Issue 12, 1997, Pages 1393-1400

  Havenga, M ^a   Fisher, R ^b   Hoogerbrugge, P ^b,c   Roberts, B ^d   Valerio, D ^a,b   Van Es, H H G ^a,b,e  

^a LEIDEN UNIVERSITY MEDICAL CENTER   (Netherlands)

^b CRUCELL HOLLAND BV   (Netherlands)

^c SOPHIA CHILDREN S HOSPITAL   (Netherlands)

^d GENZYME CORPORATION   (United States)

^e InlmGene BV   (Netherlands)

Author keywords

Gaucher disease; Gene therapy; Retrovirus

Indexed keywords

CD34 ANTIGEN; COMPLEMENTARY DNA; GLUCOSYLCERAMIDASE;

ANIMAL CELL; ARTICLE; BONE MARROW CELL; COLONY FORMING UNIT GM; CONTROLLED STUDY; DNA TRANSFER; ENZYME ACTIVITY; ENZYME DEFICIENCY; EXPRESSION VECTOR; FIBROBLAST; GAUCHER DISEASE; GENETIC TRANSDUCTION; GIBBON LEUKEMIA VIRUS; HUMAN; HUMAN CELL; MOUSE; NONHUMAN; PRIORITY JOURNAL; RETROVIRUS; VIRUS RECOMBINANT;

ALOCASIA MACRORRHIZOS; ANIMALIA; GIBBON APE LEUKEMIA VIRUS; HYLOBATES SP.; UNIDENTIFIED RETROVIRUS;

EID: 0031450903     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: 10.1038/sj.gt.3300532     Document Type: Article

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