Enzyme replacement therapy in mucopolysaccharidosis VI: Evidence for immune responses and altered efficacy of treatment in animal models

Biochimica et Biophysica Acta - Molecular Basis of Disease

Volumn 1361, Issue 2, 1997, Pages 203-216

  Brooks, Doug A ^a   King, Barbara M ^a   C Crawley, Allison ^a   Byers, Sharon ^a   Hopwood, John J ^a  

^a Lysosomal Diseases Research Unit   (Australia)

Author keywords

Antibody; Immune reaction; Lysosomal storage disease; Mucopolysaccharidosis VI; Treatment outcome

Indexed keywords

N ACETYLGALACTOSAMINE 4 SULFATASE; RECOMBINANT ENZYME;

ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; ENZYME REPLACEMENT; IMMUNITY; MAROTEAUX LAMY SYNDROME; NONHUMAN; PRIORITY JOURNAL; RAT; SUBCUTANEOUS DRUG ADMINISTRATION;

ANIMALS; ANTIBODIES; ANTIBODY FORMATION; ANXIETY; CATS; CYANOSIS; DOSE-RESPONSE RELATIONSHIP, DRUG; FEVER; HUMANS; MUCOPOLYSACCHARIDOSIS VI; N-ACETYLGALACTOSAMINE-4-SULFATASE; RATS; RECOMBINANT PROTEINS; RESPIRATION; SULFATASES; TISSUE DISTRIBUTION; VOMITING;

ANIMALIA; FELIDAE; FELIS CATUS;

EID: 0030791383     PISSN: 09254439     EISSN: None     Source Type: Journal    
DOI: 10.1016/S0925-4439(97)00036-7     Document Type: Article

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