A bicistronic therapeutic retroviral vector enables sorting of transduced CD34+ cells and corrects the enzyme deficiency in cells from Gaucher patients

Blood

Volumn 87, Issue 5, 1996, Pages 1754-1762

  Medin, Jeffrey A ^a   Migita, Makoto ^b   Pawliuk, Robert ^b   Jacobson, Steven ^b   Amiri, Mike ^b   Kluepfel Stahl, Stefanie ^b   Brady, Roscoe O ^b   Humphries, R Keith ^b   Karlsson, Stefan ^b  

^a NATIONAL INSTITUTE OF NEUROLOGICAL DISORDERS AND STROKE   (United States)

^b NONE

Author keywords

[No Author keywords available]

Indexed keywords

CD34 ANTIGEN; COMPLEMENTARY DNA; GLUCOSYLCERAMIDASE; VIRUS DNA; VIRUS VECTOR;

ANIMAL CELL; ARTICLE; CELL SELECTION; CONTROLLED STUDY; ENZYME ACTIVITY; ENZYME DEFICIENCY; FLOW CYTOMETRY; GAUCHER DISEASE; GENE TRANSFER; GENETIC TRANSDUCTION; HUMAN; HUMAN CELL; MOUSE; NONHUMAN; PRIORITY JOURNAL; RETROVIRUS; SKIN FIBROBLAST;

EID: 0030028313     PISSN: 00064971     EISSN: None     Source Type: Journal    
DOI: 10.1182/blood.v87.5.1754.1754     Document Type: Article

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