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Volumn 173, Issue 1, 2018, Pages 5-

Gene Therapy for Retinal Degeneration

Author keywords

[No Author keywords available]

Indexed keywords

11 CIS RETINAL; COMPLEMENTARY DNA; HYDROLASE; ISOMEROHYDROLASE; RETINOIC ACID; UNCLASSIFIED DRUG; VORETIGENE NEPARVOVEC; CIS TRANS ISOMERASE; RETINOID ISOMEROHYDROLASE;

EID: 85044132232     PISSN: 00928674     EISSN: 10974172     Source Type: Journal    
DOI: 10.1016/j.cell.2018.03.021     Document Type: Short Survey
Times cited : (55)

References (9)
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    • Molecular genetics and emerging therapies for retinitis pigmentosa: Basic research and clinical perspectives
    • Dias, M.F., Joo, K., Kemp, J.A., Fialho, S.L., da Silva Cunha, A. Jr., Woo, S.J., Kwon, Y.J., Molecular genetics and emerging therapies for retinitis pigmentosa: Basic research and clinical perspectives. Prog. Retin. Eye Res., 2017, 10.1016/j.preteyeres.2017.10.004.
    • (2017) Prog. Retin. Eye Res.
    • Dias, M.F.1    Joo, K.2    Kemp, J.A.3    Fialho, S.L.4    da Silva Cunha, A.5    Woo, S.J.6    Kwon, Y.J.7
  • 4
    • 0027242119 scopus 로고
    • Molecular cloning and expression of RPE65, a novel retinal pigment epithelium-specific microsomal protein that is post-transcriptionally regulated in vitro
    • Hamel, C.P., Tsilou, E., Pfeffer, B.A., Hooks, J.J., Detrick, B., Redmond, T.M., Molecular cloning and expression of RPE65, a novel retinal pigment epithelium-specific microsomal protein that is post-transcriptionally regulated in vitro. J. Biol. Chem. 268 (1993), 15751–15757.
    • (1993) J. Biol. Chem. , vol.268 , pp. 15751-15757
    • Hamel, C.P.1    Tsilou, E.2    Pfeffer, B.A.3    Hooks, J.J.4    Detrick, B.5    Redmond, T.M.6
  • 5
    • 23744447355 scopus 로고    scopus 로고
    • Rpe65 is the retinoid isomerase in bovine retinal pigment epithelium
    • Jin, M., Li, S., Moghrabi, W.N., Sun, H., Travis, G.H., Rpe65 is the retinoid isomerase in bovine retinal pigment epithelium. Cell 122 (2005), 449–459.
    • (2005) Cell , vol.122 , pp. 449-459
    • Jin, M.1    Li, S.2    Moghrabi, W.N.3    Sun, H.4    Travis, G.H.5
  • 7
    • 85023744466 scopus 로고    scopus 로고
    • Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial
    • Russell, S., Bennett, J., Wellman, J.A., Chung, D.C., Yu, Z.F., Tillman, A., Wittes, J., Pappas, J., Elci, O., McCague, S., et al. Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial. Lancet 390 (2017), 849–860.
    • (2017) Lancet , vol.390 , pp. 849-860
    • Russell, S.1    Bennett, J.2    Wellman, J.A.3    Chung, D.C.4    Yu, Z.F.5    Tillman, A.6    Wittes, J.7    Pappas, J.8    Elci, O.9    McCague, S.10
  • 9
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    • 2017 Meeting Materials, Cellular, Tissue and Gene Therapies Advisory Committee.
    • Food and Drug Administration. 2017 Meeting Materials, Cellular, Tissue and Gene Therapies Advisory Committee. https://www.fda.gov/AdvisoryCommittees/CommitteesMeetingMaterials/BloodVaccinesandOtherBiologics/CellularTissueandGeneTherapiesAdvisoryCommittee/ucm574396.htm.


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.