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Volumn 60, Issue 1, 2018, Pages 13-18
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Treatment strategies for lysosomal storage disorders
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Author keywords
[No Author keywords available]
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Indexed keywords
CHAPERONE;
RECOMBINANT ENZYME;
CRISPR-CAS9 SYSTEM;
ENZYME DEFICIENCY;
ENZYME REPLACEMENT;
EX VIVO STUDY;
GENE THERAPY;
HEMATOPOIETIC STEM CELL TRANSPLANTATION;
HUMAN;
IN VIVO STUDY;
LYSOSOME STORAGE DISEASE;
NEWBORN SCREENING;
NONHUMAN;
PRIORITY JOURNAL;
REVIEW;
STOP CODON;
SYMPTOMATOLOGY;
PROCEDURES;
ENZYME REPLACEMENT THERAPY;
GENETIC THERAPY;
HEMATOPOIETIC STEM CELL TRANSPLANTATION;
HUMANS;
LYSOSOMAL STORAGE DISEASES;
MOLECULAR CHAPERONES;
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EID: 85032808893
PISSN: 00121622
EISSN: 14698749
Source Type: Journal
DOI: 10.1111/dmcn.13600 Document Type: Review |
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Times cited : (86)
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References (0)
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