Allogeneic cellular gene therapy in hemoglobinopathiesevaluation of hematopoietic SCT in sickle cell anemia

Bone Marrow Transplantation

Volumn 47, Issue 2, 2012, Pages 227-230

  Lucarelli, G ^a   Gaziev, J ^a   Isgro A ^a   Sodani, P ^a   Paciaroni, K ^a   Alfieri, C ^a   De Angelis, G ^a   Marziali, M ^a   Simone, M D ^a   Gallucci, C ^a   Roveda, A ^a   Saltarelli, F ^a   Torelli, F ^a   Andreani, M ^a  

^a TOR VERGATA UNIVERSITY HOSPITAL   (Italy)

Author keywords

hemoglobinopathy; sickle cell anemia; transplantation

Indexed keywords

ANTIBIOTIC AGENT; CYCLOSPORIN A; FK 500; GANCICLOVIR; MEPREDNISONE; TACROLIMUS; UNCLASSIFIED DRUG;

ACUTE CHEST SYNDROME; ACUTE GRAFT VERSUS HOST DISEASE; ADOLESCENT; ALLOGENEIC STEM CELL TRANSPLANTATION; ARTICLE; AVASCULAR NECROSIS; BACTERIAL INFECTION; BK VIRUS; BLOOD TRANSFUSION; BRAIN HEMORRHAGE; CHILD; CHRONIC GRAFT VERSUS HOST DISEASE; CLINICAL ARTICLE; CLINICAL EVALUATION; CONTROLLED STUDY; CYTOMEGALOVIRUS INFECTION; DISEASE FREE SURVIVAL; DISEASE SEVERITY; DRUG SUBSTITUTION; DRUG WITHDRAWAL; ENGRAFTMENT; FEMALE; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMOGLOBINOPATHY; HEMORRHAGIC CYSTITIS; HLA TYPING; HUMAN; KARNOFSKY PERFORMANCE STATUS; LOW DRUG DOSE; MALE; MYELOABLATIVE CONDITIONING; NEUROTOXICITY; PRESCHOOL CHILD; PRIORITY JOURNAL; SCHOOL CHILD; SEIZURE; SICKLE CELL ANEMIA; STEM CELL GENE THERAPY; SURVIVAL RATE; TREATMENT INDICATION; TREATMENT OUTCOME; VIRUS INFECTION;

EID: 85028101011     PISSN: 02683369     EISSN: 14765365     Source Type: Journal    
DOI: 10.1038/bmt.2011.79     Document Type: Article

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