Hematopoietic stem cell transplantation in patients with gain-of-function signal transducer and activator of transcription 1 mutations

Journal of Allergy and Clinical Immunology

Volumn 141, Issue 2, 2018, Pages 704-717.e5

  Leiding, Jennifer W ^a   Okada, Satoshi ^b   Hagin, David ^c   Abinun, Mario ^d,e   Shcherbina, Anna ^f   Balashov, Dmitry N ^f   Kim, Vy H D ^g   Ovadia, Adi ^g   Guthery, Stephen L ^h   Pulsipher, Michael ⁱ   Lilic, Desa ^e   Devlin, Lisa A ^j   Christie, Sharon ^j   Depner, Mark ^k   Fuchs, Sebastian ^k   van Royen Kerkhof, Annet ^l   Lindemans, Caroline ^l   Petrovic, Aleksandra ^c,m   Sullivan, Kathleen E ⁿ   Bunin, Nancy ⁿ   Kilic, Sara Sebnem ^o   Arpaci, Fikret ^p   Calle Martin, Oscar de la ^q   Martinez Martinez, Laura ^q   Aldave, Juan Carlos ^r   Kobayashi, Masao ^b   Ohkawa, Teppei ^s   Imai, Kohsuke ^s   Iguchi, Akihiro ^t   Roifman, Chaim M ^g   Gennery, Andrew R ^d,e   Slatter, Mary ^d,e   Ochs, Hans D ^c   Morio, Tomohiro ^s   Torgerson, Troy R ^c,u   more..

^a UNIVERSITY OF SOUTH FLORIDA   (United States)

^b HIROSHIMA UNIVERSITY   (Japan)

^c UNIVERSITY OF WASHINGTON   (United States)

^d Newcastle Upon Tyne Hospitals NHS Foundation Trust   (United Kingdom)

^e NEWCASTLE UNIVERSITY   (United Kingdom)

^f Clinical and Research Center for Allergy and Immunology   (Russian Federation)

^g HOSPITAL FOR SICK CHILDREN   (Canada)

^h UNIVERSITY OF UTAH SCHOOL OF MEDICINE   (United States)

ⁱ UNIVERSITY OF SOUTHERN CALIFORNIA   (United States)

^j ROYAL VICTORIA HOSPITAL   (United Kingdom)

^k UNIVERSITY OF FREIBURG   (Germany)

^l UNIVERSITY MEDICAL CENTER UTRECHT   (Netherlands)

^m JOHNS HOPKINS ALL CHILDREN S HOSPITAL   (United States)

ⁿ UNIVERSITY OF PENNSYLVANIA   (United States)

^o ULUDAG UNIVERSITY   (Turkey)

^p GULHANE SCHOOL OF MEDICINE   (Turkey)

^q HOSPITAL DE LA SANTA CREU I SANT PAU   (Spain)

^r HOSPITAL NACIONAL EDGARDO REBAGLIATI MARTINS   (Peru)

^s TOKYO MEDICAL AND DENTAL UNIVERSITY   (Japan)

^t HOKKAIDO UNIVERSITY GRADUATE SCHOOL OF MEDICINE   (Japan)

^u SEATTLE CHILDREN S RESEARCH INSTITUTE   (United States)

more..

Author keywords

chronic mucocutaneous candidiasis; gain of function; graft rejection; graft versus host disease; Hematopoietic stem cell transplantation; hemophagocytic lymphohistiocytosis; Janus kinase; signal transducer and activator of transcription

Indexed keywords

ALEMTUZUMAB; BUSULFAN; CYCLOPHOSPHAMIDE; ETOPOSIDE; FLUDARABINE; MELPHALAN; RITUXIMAB; RUXOLITINIB; STAT1 PROTEIN; THYMOCYTE ANTIBODY; TREOSULFAN; STAT1 PROTEIN, HUMAN;

ADOLESCENT; ADULT; ARTICLE; CATHETER THROMBOSIS; CHILD; CLINICAL ARTICLE; COHORT ANALYSIS; ENGRAFTMENT; EVENT FREE SURVIVAL; FEMALE; GAIN OF FUNCTION MUTATION; GASTROINTESTINAL HEMORRHAGE; GRAFT FAILURE; GRAFT VERSUS HOST REACTION; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMOPHAGOCYTIC SYNDROME; HEPATITIS; HUMAN; IN VITRO STUDY; LUNG EDEMA; MALE; OUTCOME ASSESSMENT; OVERALL SURVIVAL; PANCREATITIS; PRIORITY JOURNAL; RETROSPECTIVE STUDY; SUPRAVENTRICULAR TACHYCARDIA; TRANSPLANTATION CONDITIONING; WHOLE BODY RADIATION; ALLOGRAFT; DISEASE FREE SURVIVAL; GENETIC PREDISPOSITION; GENETICS; IMMUNOLOGY; MORTALITY; RISK FACTOR; SURVIVAL RATE;

ALLOGRAFTS; DISEASE-FREE SURVIVAL; FEMALE; GAIN OF FUNCTION MUTATION; GENETIC PREDISPOSITION TO DISEASE; GRAFT VS HOST DISEASE; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMANS; MALE; RETROSPECTIVE STUDIES; RISK FACTORS; STAT1 TRANSCRIPTION FACTOR; SURVIVAL RATE;

EID: 85025832226     PISSN: 00916749     EISSN: 10976825     Source Type: Journal    
DOI: 10.1016/j.jaci.2017.03.049     Document Type: Article

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