A systematic review of the prevalence of Morquio A syndrome: challenges for study reporting in rare diseases

Orphanet journal of rare diseases

Volumn 9, Issue , 2014, Pages 173-

  Leadley, Regina M ^a   Lang, Shona ^a   Misso, Kate ^a   Bekkering, Trudy ^a   Ross, Janine ^a   Akiyama, Takeyuki ^a   Fietz, Michael ^a   Giugliani, Roberto ^a   Hendriksz, Chris J ^a   Hock, Ngu Lock ^a   McGill, Jim ^a   Olaye, Andrew ^b   Jain, Mohit ^b   Kleijnen, Jos ^a  

^a MAASTRICHT UNIVERSITY   (Netherlands)

^b BIOMARIN PHARMACEUTICAL INC   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

CLINICAL TRIAL; HUMAN; MUCOPOLYSACCHARIDOSIS IV; MULTICENTER STUDY; PREVALENCE; RARE DISEASE;

HUMANS; MUCOPOLYSACCHARIDOSIS IV; PREVALENCE; RARE DISEASES;

EID: 85017330959     PISSN: None     EISSN: 17501172     Source Type: Journal    
DOI: 10.1186/s13023-014-0173-x     Document Type: Article

References (0)