Agalsidase alfa in pediatric patients with Fabry disease: a 6.5-year open-label follow-up study

Orphanet journal of rare diseases

Volumn 9, Issue , 2014, Pages 169-

  Schiffmann, Raphael ^a   Pastores, Gregory M ^a   Lien, Yeong Hau H ^a   Castaneda, Victoria ^a   Chang, Peter ^a   Martin, Rick ^a   Wijatyk, Anna ^a  

^a SHIRE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

AGALSIDASE ALFA; ALPHA GALACTOSIDASE; ISOENZYME;

ADOLESCENT; ADVERSE EFFECTS; CHILD; CLINICAL TRIAL; ENZYME REPLACEMENT; FABRY DISEASE; FEMALE; FOLLOW UP; HUMAN; MALE; MULTICENTER STUDY; PHASE 1 CLINICAL TRIAL; PHASE 2 CLINICAL TRIAL; PROCEDURES; TREATMENT OUTCOME;

ADOLESCENT; ALPHA-GALACTOSIDASE; CHILD; ENZYME REPLACEMENT THERAPY; FABRY DISEASE; FEMALE; FOLLOW-UP STUDIES; HUMANS; ISOENZYMES; MALE; TREATMENT OUTCOME;

EID: 85017330287     PISSN: None     EISSN: 17501172     Source Type: Journal    
DOI: 10.1186/s13023-014-0169-6     Document Type: Article

References (0)