Long-term cognitive and functional outcomes in children with mucopolysaccharidosis (MPS)-IH (Hurler Syndrome) treated with hematopoietic cell transplantation

JIMD Reports

Volumn 29, Issue , 2016, Pages 95-102

  Kunin Batson, A S ^a,b   Shapiro, E G ^b   Rudser, K D ^c   Lavery, C A ^d   Bjoraker, K J ^e   Jones, S A ^f   Wynn, R F ^f   Vellodi, A ^g   Tolar, J ^b   Orchard, P J ^b   Wraith, J E ^f  

^a HEALTHPARTNERS INSTITUTE   (United States)

^b UNIVERSITY OF MINNESOTA MEDICAL SCHOOL   (United States)

^c UNIVERSITY OF MINNESOTA   (United States)

^d Society for Mucopolysaccharide Disease   (United Kingdom)

^e Box 390   (United States)

^f ROYAL MANCHESTER CHILDREN S HOSPITAL   (United Kingdom)

^g GREAT ORMOND STREET HOSPITAL   (United Kingdom)

Author keywords

Adaptive Functioning; Adaptive Skill; Hematopoietic Cell Transplantation; Mutation Type; Total Body Irradiation

Indexed keywords

EID: 85013694925     PISSN: 21928304     EISSN: 21928312     Source Type: Book Series    
DOI: 10.1007/8904_2015_521     Document Type: Chapter

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