Investor Outlook: Solving Gene Therapy Pricing...with a Cures Voucher?

Human Gene Therapy Clinical Development

Volumn 27, Issue 4, 2016, Pages 132-136

  Schimmer, Joshua ^a   Breazzano, Steven ^a  

^a Piper Jaffray Company   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ARTICLE; COMMERCIAL PHENOMENA; GENE THERAPY; HEALTH CARE COST; HUMAN; INVESTMENT; PRIORITY JOURNAL; QUALITY CONTROL; REIMBURSEMENT; COST; DRUG INDUSTRY; ECONOMICS;

COSTS AND COST ANALYSIS; DRUG INDUSTRY; GENETIC THERAPY; HUMANS; INSURANCE, HEALTH, REIMBURSEMENT; INVESTMENTS;

EID: 85006826187     PISSN: 23248637     EISSN: 23248645     Source Type: Journal    
DOI: 10.1089/humc.2016.29018.ind     Document Type: Article

References (7)

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3. Schimmer J, Breazzano S. Investor outlook: Rising from the ashes; GSK's European approval of Strimvelis for ADA-SCID. Hum Gene Ther Clin Dev 2016;27:57-61.
4. STAT. There's a possible cure for ''bubble boy'' disease. It will cost 665, 000. Available from: https://www.statnews.com/2016/08/03/gene-therapyprice- gsk/ (last accessed November 6, 2016).
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6. STAT. FDA wants to nix voucher program for rare pediatric disease drugs. Available from: https:// www.statnews.com/pharmalot/2016/03/03/fdapediatric- disease-gao/ (last accessed November 6, 2016).
7. Regulatory Affairs Professionals Society. Regulatory explainer: The (updated) 21st Century Cures Act. Available from: http://www.raps.org/Regulatory- Focus/News/2015/04/30/21192/Regulatory-Explainer- The-Updated-21st-Century-Cures-Act/ (last accessed November 6, 2016).