Preclinical safety evaluation of a recombinant AAV8 vector for X-linked retinoschisis after intravitreal administration in rabbits

Human gene therapy. Clinical development

Volumn 25, Issue 4, 2014, Pages 202-211

  Marangoni, Dario ^a   Wu, Zhijian ^a   Wiley, Henry E ^a   Zeiss, Caroline J ^a   Vijayasarathy, Camasamudram ^a   Zeng, Yong ^a   Hiriyanna, Suja ^a   Bush, Ronald A ^a   Wei, Lisa L ^a   Colosi, Peter ^a   Sieving, Paul A ^a  

^a NATIONAL INSTITUTE ON DEAFNESS AND OTHER COMMUNICATION DISORDERS   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

EYE PROTEIN; RECOMBINANT DNA; RS1 PROTEIN, HUMAN;

ADMINISTRATION AND DOSAGE; ADVERSE EFFECTS; ANIMAL; DEPENDOPARVOVIRUS; GENE THERAPY; GENE VECTOR; GENETICS; INTRAVITREAL DRUG ADMINISTRATION; METABOLISM; RABBIT; RETINOSCHISIS;

ANIMALS; DEPENDOVIRUS; DNA, RECOMBINANT; EYE PROTEINS; GENETIC THERAPY; GENETIC VECTORS; INTRAVITREAL INJECTIONS; RABBITS; RETINOSCHISIS;

EID: 84964698736     PISSN: None     EISSN: 23248645     Source Type: Journal    
DOI: 10.1089/humc.2014.067     Document Type: Article

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