Drugs in development and dietary approach for duchenne muscular dystrophy

Orphan Drugs: Research and Reviews

Volumn 5, Issue , 2015, Pages 51-60

  Angelini, Corrado ^a   Tasca, Elisabetta ^a  

^a IRCCS SAN CAMILLO HOSPITAL   (Italy)

Author keywords

Ataluren; Drisapersen; Duchenne muscular dystrophy; Eplerenone; Eteplirsen; Steroids

Indexed keywords

ATALUREN; DEFLAZACORT; DRISAPERSEN; DYSTROPHIN; EPLERENONE; ETEPLIRSEN; GENTAMICIN; GIVINOSTAT; NITRIC OXIDE SYNTHASE; OXANDROLONE; SILDENAFIL;

ANTIBODY LABELING; ARTICLE; DISEASE SEVERITY; DUCHENNE MUSCULAR DYSTROPHY; GENE MUTATION; GENETIC DISORDER; HISTOPATHOLOGY; IMMUNOHISTOCHEMISTRY; MUSCLE WEAKNESS; QUALITY OF LIFE; SARCOLEMMA;

EID: 84959370487     PISSN: None     EISSN: 22306161     Source Type: Journal    
DOI: 10.2147/ODRR.S55677     Document Type: Article

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