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Volumn 169, Issue , 2016, Pages 174-180.e1

Very Early Treatment for Infantile-Onset Pompe Disease Contributes to Better Outcomes

Author keywords

AST Aspartate aminotransferase; Bayley III Bayley Scale of Infant and Toddler Development, Third Edition; CK Creatine kinase; CRIM Cross reactive immunologic; ERT Enzyme replacement therapy; GAA Acid glucosidase; IOPD Infantile onset Pompe disease; LDH Lactate dehydrogenase; LVMI Left ventricular mass index; PDMS II Peabody Development Motor Scale, Second Edition; TVGH Taipei Veterans General Hospital

Indexed keywords

ALPHA GLUCOSIDASE ANTIBODY; ANTIBODY; RHESUS ANTIBODY; UNCLASSIFIED DRUG; GLUCAN 1,4 ALPHA GLUCOSIDASE;

EID: 84959307776     PISSN: 00223476     EISSN: 10976833     Source Type: Journal    
DOI: 10.1016/j.jpeds.2015.10.078     Document Type: Article
Times cited : (87)

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