Thalassemia: A look to the future

Annals of the New York Academy of Sciences

Volumn 1368, Issue 1, 2016, Pages 11-15

  Nathan, David G ^a  

^a DANA FARBER CANCER INSTITUTE   (United States)

Author keywords

Gene therapy; Hemoglobin; Sickle cell disease; Thalassemia

Indexed keywords

DEFERIPRONE; DEFEROXAMINE; HEMOGLOBIN F; HYDROXYUREA; SIDEROPHORE;

ARTICLE; BLOOD BRAIN BARRIER; CLINICAL TRIAL (TOPIC); DISEASE SEVERITY; DRUG HALF LIFE; ENHANCER REGION; ERYTHROCYTE TRANSFUSION; GENE THERAPY; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; IRON CHELATION; IRON OVERLOAD; MOLECULAR BIOLOGY; MOLECULAR PATHOLOGY; PROTEIN EXPRESSION; SICKLE CELL ANEMIA; STEM CELL TRANSPLANTATION; THALASSEMIA; THALASSEMIA INTERMEDIA; THALASSEMIA MAJOR; ANIMAL; BIOSYNTHESIS; FORECASTING; GENETICS; METABOLISM; ORGANIZATION; PEDIGREE; PROCEDURES; TRENDS;

ANIMALS; CONGRESSES AS TOPIC; FETAL HEMOGLOBIN; FORECASTING; GENETIC THERAPY; HUMANS; PEDIGREE; STEM CELL TRANSPLANTATION; THALASSEMIA;

EID: 84958212481     PISSN: 00778923     EISSN: 17496632     Source Type: Journal    
DOI: 10.1111/nyas.13002     Document Type: Article

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