Prolonged ambulation in duchenne patients with a mutation amenable to exon 44 skipping

Journal of Neuromuscular Diseases

Volumn 1, Issue 1, 2014, Pages 91-94

  van den Bergen, J C ^a   Ginjaar, H B ^a   Niks, E H ^a   Aartsma Rus, A ^a   Verschuuren, J J G M ^a  

^a LEIDEN UNIVERSITY MEDICAL CENTER   (Netherlands)

Author keywords

Disease progression; Duchenne muscular dystrophy; Exon skipping

Indexed keywords

DYSTROPHIN;

ADOLESCENT; ARTICLE; CHILD; COHORT ANALYSIS; CONTROLLED STUDY; DISEASE COURSE; DMD GENE; DUCHENNE MUSCULAR DYSTROPHY; EXON SKIPPING; GENE DELETION; GENE MUTATION; HUMAN; MAJOR CLINICAL STUDY; PRIORITY JOURNAL; RETROSPECTIVE STUDY;

EID: 84949954964     PISSN: 22143599     EISSN: 22143602     Source Type: Journal    
DOI: 10.3233/JND-140002     Document Type: Article

References (10)

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