Development and psychometric analysis of the Duchenne muscular dystrophy Functional Ability Self-Assessment Tool (DMDSAT)

Neuromuscular Disorders

Volumn 25, Issue 12, 2015, Pages 937-944

  Landfeldt, Erik ^a,b   Mayhew, Anna ^c   Eagle, Michelle ^c   Lindgren, Peter ^b   Bell, Christopher F ^d   Guglieri, Michela ^c   Straub, Volker ^c   Lochmüller, Hanns ^c   Bushby, Katharine ^c  

^a OptumInsight   (Sweden)

^b KAROLINSKA INSTITUTE   (Sweden)

^c NEWCASTLE UNIVERSITY   (United Kingdom)

^d GLAXOSMITHKLINE   (United States)

Author keywords

Costs; Functional ability; Patient reported outcome; Rasch analysis; Rating scale; Utilities

Indexed keywords

ADOLESCENT; ADULT; ARTICLE; CAREGIVER; CHILD; COST OF ILLNESS; DUCHENNE MUSCULAR DYSTROPHY; DUCHENNE MUSCULAR DYSTROPHY FUNCTIONAL ABILITY SELF-ASSESSMENTTOOL; FUNCTIONAL STATUS; HEALTH ECONOMICS; HUMAN; MAJOR CLINICAL STUDY; MEDICAL SPECIALIST; OUTCOME ASSESSMENT; PRESCHOOL CHILD; PRIORITY JOURNAL; PSYCHOMETRY; QUALITY OF LIFE; RASCH ANALYSIS; RATING SCALE; RELIABILITY; SCHOOL CHILD; SCORING SYSTEM; SELF EVALUATION; SELF REPORT; UNITED KINGDOM; DAILY LIFE ACTIVITY; ECONOMICS; FEMALE; MALE; MUSCULAR DYSTROPHY, DUCHENNE; QUESTIONNAIRE; YOUNG ADULT;

ACTIVITIES OF DAILY LIVING; ADOLESCENT; ADULT; CAREGIVERS; CHILD; CHILD, PRESCHOOL; DIAGNOSTIC SELF EVALUATION; FEMALE; HUMANS; MALE; MUSCULAR DYSTROPHY, DUCHENNE; PSYCHOMETRICS; QUALITY OF LIFE; SURVEYS AND QUESTIONNAIRES; YOUNG ADULT;

EID: 84949523520     PISSN: 09608966     EISSN: 18732364     Source Type: Journal    
DOI: 10.1016/j.nmd.2015.09.012     Document Type: Article

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