Effectiveness of agalsidase alfa enzyme replacement in Fabry disease: cardiac outcomes after 10 years' treatment

Orphanet Journal of Rare Diseases

Volumn 10, Issue 1, 2015, Pages

  Kampmann, Christoph ^a   Perrin, Amandine ^b   Beck, Michael ^a  

^a JOHANNES GUTENBERG UNIVERSITY   (Germany)

^b Statistical Programmer Rare Diseases Business Unit Global Outcomes Research Shire   (Switzerland)

Author keywords

Agalsidase alfa; Cardiomyopathy; Enzyme replacement therapy; Fabry disease; Left ventricular hypertrophy; Lysosomal storage disorder

Indexed keywords

AGALSIDASE ALFA; BETA ADRENERGIC RECEPTOR BLOCKING AGENT; DIPEPTIDYL CARBOXYPEPTIDASE INHIBITOR; ALPHA GALACTOSIDASE; ISOENZYME;

ADOLESCENT; ADULT; ANGINA PECTORIS; ARTICLE; CARDIOMYOPATHY; CLINICAL ARTICLE; CONTROLLED STUDY; DRUG EFFECT; DRUG EFFICACY; DUAL CHAMBER PACEMAKER; END STAGE RENAL DISEASE; ENZYME REPLACEMENT; FABRY DISEASE; FEMALE; GERMANY; HEART FAILURE; HEART FUNCTION; HEART LEFT VENTRICLE HYPERTROPHY; HEART LEFT VENTRICLE MASS; HUMAN; KIDNEY FUNCTION; MALE; MEDICAL RECORD REVIEW; RENAL REPLACEMENT THERAPY; RETROSPECTIVE STUDY; TRANSLUMINAL CORONARY ANGIOPLASTY; TREATMENT DURATION; TREATMENT OUTCOME; CARDIOMYOPATHIES; MIDDLE AGED; PROSPECTIVE STUDY; TIME FACTOR; TRENDS; YOUNG ADULT;

ADULT; ALPHA-GALACTOSIDASE; CARDIOMYOPATHIES; ENZYME REPLACEMENT THERAPY; FABRY DISEASE; FEMALE; GERMANY; HUMANS; ISOENZYMES; MALE; MIDDLE AGED; PROSPECTIVE STUDIES; RETROSPECTIVE STUDIES; TIME FACTORS; TREATMENT OUTCOME; YOUNG ADULT;

EID: 84942410880     PISSN: None     EISSN: 17501172     Source Type: Journal    
DOI: 10.1186/s13023-015-0338-2     Document Type: Article

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