Old measures and new scores in spinal muscular atrophy patients

Muscle and Nerve

Volumn 52, Issue 3, 2015, Pages 435-437

  Mazzone, Elena ^a   Montes, Jacqueline ^b   Main, Marion ^c   Mayhew, Anna ^d   Ramsey, Danielle ^c   Glanzman, Allan M ^e   Dunaway, Sally ^b   Salazar, Rachel ^b   Pasternak, Amy ^f   Quigley, Janet ^f   Pane, Marika ^a   Pera, Maria C ^a   Scoto, Mariacristina ^c   Messina, Sonia ^g   Sframeli, Maria ^g   D'amico, Adele ^h   Van Den Hauwe, Marleen ⁱ   Sivo, Serena ^a   Goemans, Nathalie ⁱ   Darras, Basil T ^f   Kaufmann, Petra ^b   Bertini, Enrico ^h   De Vivo, Darryl C ^b   Muntoni, Francesco ^c   Finkel, Richard ^j   Mercuri, Eugenio ^a,c   more..

^a CATHOLIC UNIVERSITY   (Italy)

^b Department of Medicine   (United States)

^c UNIVERSITY COLLEGE LONDON   (United Kingdom)

^d NEWCASTLE UNIVERSITY   (United Kingdom)

^e CHILDREN S HOSPITAL OF PHILADELPHIA   (United States)

^f HARVARD MEDICAL SCHOOL   (United States)

^g UNIVERSITY OF MESSINA   (Italy)

^h BAMBINO GESÙ CHILDREN S HOSPITAL   (Italy)

ⁱ UNIVERSITY HOSPITALS LEUVEN   (Belgium)

^j UNIVERSITY OF CENTRAL FLORIDA COLLEGE OF MEDICINE   (United States)

more..

Author keywords

Neuromuscular; Outcome measures; Rasch analysis; Scoring; Spinal muscular atrophy

Indexed keywords

ADOLESCENT; ADULT; ARTICLE; CHILD; CLINICAL ASSESSMENT TOOL; CONSENSUS; HAMMERSMITH FUNCTIONAL MOTOR SCALE EXPANDED; HUMAN; MAJOR CLINICAL STUDY; PRIORITY JOURNAL; RASCH ANALYSIS; RETROSPECTIVE STUDY; SCORING SYSTEM; SPINAL MUSCULAR ATROPHY; VALIDITY; FEMALE; HEREDITARY SPINAL MUSCULAR ATROPHY; MALE; MIDDLE AGED; PATHOPHYSIOLOGY; PRESCHOOL CHILD; PSYCHOMETRY; SEVERITY OF ILLNESS INDEX; YOUNG ADULT;

ADOLESCENT; ADULT; CHILD; CHILD, PRESCHOOL; FEMALE; HUMANS; MALE; MIDDLE AGED; MUSCULAR ATROPHY, SPINAL; PSYCHOMETRICS; RETROSPECTIVE STUDIES; SEVERITY OF ILLNESS INDEX; SPINAL MUSCULAR ATROPHIES OF CHILDHOOD; YOUNG ADULT;

EID: 84938982221     PISSN: 0148639X     EISSN: 10974598     Source Type: Journal    
DOI: 10.1002/mus.24748     Document Type: Article

References (15)

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