New approaches to gene and cell therapy for hemophilia

Journal of Thrombosis and Haemostasis

Volumn 13, Issue S1, 2015, Pages S133-S142

  Ohmori, T ^a   Mizukami, H ^a   Ozawa, K ^b   Sakata, Y ^a   Nishimura, S ^a,b  

^a JICHI MEDICAL UNIVERSITY   (Japan)

^b UNIVERSITY OF TOKYO   (Japan)

Author keywords

Cell therapy; Gene therapy; Genetic; Hemophilia; Vectors; Viruses, adeno associated

Indexed keywords

BLOOD CLOTTING FACTOR 8; BLOOD CLOTTING FACTOR 9; BLOOD CLOTTING INHIBITOR; LENTIVIRUS VECTOR; PARVOVIRUS VECTOR; RETROVIRUS VECTOR;

ADIPOCYTE; BLOOD CLOTTING; CELL THERAPY; CELL TRANSPLANTATION; ENDOTHELIUM CELL; FIBROBLAST; GENE THERAPY; GENE VECTOR; HEMOPHILIA; HEMOPHILIA A; HEMOPHILIA B; HUMAN; LIVER CELL; MESENCHYMAL STEM CELL; NONHUMAN; PHASE 1 CLINICAL TRIAL (TOPIC); PHASE 2 CLINICAL TRIAL (TOPIC); PRIORITY JOURNAL; PROTEIN EXPRESSION; PROTEIN TARGETING; QUALITY OF LIFE; REVIEW; THERAPY EFFECT; ANIMAL; BLOOD; DEPENDOPARVOVIRUS; GENE TRANSFER; GENETIC PREDISPOSITION; GENETICS; HEMORRHAGE; PHENOTYPE; PROCEDURES;

ANIMALS; BLOOD COAGULATION; DEPENDOVIRUS; GENE TRANSFER TECHNIQUES; GENETIC PREDISPOSITION TO DISEASE; GENETIC THERAPY; GENETIC VECTORS; HEMOPHILIA A; HEMORRHAGE; HUMANS; PHENOTYPE;

EID: 84931345313     PISSN: 15387933     EISSN: 15387836     Source Type: Journal    
DOI: 10.1111/jth.12926     Document Type: Review

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