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Volumn 125, Issue 23, 2015, Pages 3521-3522

Gene therapy outpaces haplo for SCID-X1

Author keywords

[No Author keywords available]

Indexed keywords

IMMUNOGLOBULIN M; INTERLEUKIN 2 RECEPTOR GAMMA; PHYTOHEMAGGLUTININ; RETROVIRUS VECTOR;

EID: 84930665543     PISSN: 00064971     EISSN: 15280020     Source Type: Journal    
DOI: 10.1182/blood-2015-04-641720     Document Type: Note
Times cited : (6)

References (8)
  • 1
    • 84930622918 scopus 로고    scopus 로고
    • Faster T-cell development following gene therapy compared with haploidentical HSCT in the treatment of SCID-X1
    • Touzot F, Moshous D, Creidy R, et al. Faster T-cell development following gene therapy compared with haploidentical HSCT in the treatment of SCID-X1. Blood. 2015;125(23):3563-3569.
    • (2015) Blood , vol.125 , Issue.23 , pp. 3563-3569
    • Touzot, F.1    Moshous, D.2    Creidy, R.3
  • 2
    • 0034724857 scopus 로고    scopus 로고
    • Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease
    • Cavazzana-Calvo M, Hacein-Bey S, de Saint Basile G, et al. Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease. Science. 2000;288(5466):669-672.
    • (2000) Science , vol.288 , Issue.5466 , pp. 669-672
    • Cavazzana-Calvo, M.1    Hacein-Bey, S.2    De Saint Basile, G.3
  • 3
    • 77954833516 scopus 로고    scopus 로고
    • Efficacy of gene therapy for X-linked severe combined immunodeficiency
    • Hacein-Bey-Abina S, Hauer J, Lim A, et al. Efficacy of gene therapy for X-linked severe combined immunodeficiency. N Engl J Med. 2010;363(4):355-364.
    • (2010) N Engl J Med , vol.363 , Issue.4 , pp. 355-364
    • Hacein-Bey-Abina, S.1    Hauer, J.2    Lim, A.3
  • 4
    • 80052048463 scopus 로고    scopus 로고
    • Long-term persistence of a polyclonal T cell repertoire after gene therapy for X-linked severe combined immunodeficiency
    • Gaspar HB, Cooray S, Gilmour KC, et al. Long-term persistence of a polyclonal T cell repertoire after gene therapy for X-linked severe combined immunodeficiency. Sci Transl Med. 2011;3(97):97ra79.
    • (2011) Sci Transl Med , vol.3 , Issue.97
    • Gaspar, H.B.1    Cooray, S.2    Gilmour, K.C.3
  • 5
    • 0142084745 scopus 로고    scopus 로고
    • LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1
    • Hacein-Bey-Abina S, Von Kalle C, Schmidt M, et al. LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1. Science. 2003;302(5644):415-419.
    • (2003) Science , vol.302 , Issue.5644 , pp. 415-419
    • Hacein-Bey-Abina, S.1    Von Kalle, C.2    Schmidt, M.3
  • 6
    • 51349158298 scopus 로고    scopus 로고
    • Insertional mutagenesis combined with acquired somatic mutations causes leukemogenesis following gene therapy of SCID-X1 patients
    • Howe SJ, Mansour MR, Schwarzwaelder K, et al. Insertional mutagenesis combined with acquired somatic mutations causes leukemogenesis following gene therapy of SCID-X1 patients. J Clin Invest. 2008;118(9):3143-3150.
    • (2008) J Clin Invest , vol.118 , Issue.9 , pp. 3143-3150
    • Howe, S.J.1    Mansour, M.R.2    Schwarzwaelder, K.3
  • 7
    • 84907880404 scopus 로고    scopus 로고
    • A modified g-retrovirus vector for X-linked severe combined immunodeficiency
    • Hacein-Bey-Abina S, Pai SY, Gaspar HB, et al. A modified g-retrovirus vector for X-linked severe combined immunodeficiency. N Engl J Med. 2014;371(15):1407-1417.
    • (2014) N Engl J Med , vol.371 , Issue.15 , pp. 1407-1417
    • Hacein-Bey-Abina, S.1    Pai, S.Y.2    Gaspar, H.B.3
  • 8
    • 21544467270 scopus 로고    scopus 로고
    • Cell intrinsic alterations underlie hematopoietic stem cell aging
    • Rossi DJ, Bryder D, Zahn JM, et al. Cell intrinsic alterations underlie hematopoietic stem cell aging. Proc Natl Acad Sci USA. 2005;102(26):9194-9199.
    • (2005) Proc Natl Acad Sci USA , vol.102 , Issue.26 , pp. 9194-9199
    • Rossi, D.J.1    Bryder, D.2    Zahn, J.M.3


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.