Should patients in need be given access to experimental drugs?

Expert Opinion on Pharmacotherapy

Volumn 16, Issue 9, 2015, Pages 1275-1279

  Caplan, Arthur L ^a   Bateman House, Alison ^a  

^a NEW YORK UNIVERSITY MEDICAL CENTER   (United States)

Author keywords

Compassionate use; Expanded access; Experimental drugs; Investigational products; Right to try

Indexed keywords

NEW DRUG;

COMPASSIONATE USE; EMERGENCY CARE; FOOD AND DRUG ADMINISTRATION; HEALTH CARE ACCESS; HEALTH CARE NEED; HEALTH CARE PERSONNEL; HEALTH CARE POLICY; HUMAN; MEDICAL ETHICS; MORALITY; PATIENT CARE; PRACTICE GUIDELINE; REVIEW; RISK BENEFIT ANALYSIS; SOCIETY; THERAPEUTIC MISCONCEPTION; DRUG APPROVAL; ETHICS; LEGISLATION AND JURISPRUDENCE; TRENDS;

COMPASSIONATE USE TRIALS; DRUGS, INVESTIGATIONAL; HEALTH POLICY; HUMANS; INVESTIGATIONAL NEW DRUG APPLICATION;

EID: 84929877519     PISSN: 14656566     EISSN: 17447666     Source Type: Journal    
DOI: 10.1517/14656566.2015.1046837     Document Type: Review

References (23)

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2. This is not the case in the 17 states that have passed so-called Right to Try laws, which will be discussed elsewhere in this editorial 3. For the most recent numbers from the FDA, see Expanded Access Submissions Receipt Report Oct 1, 2013-Sep 30, 2014. Available from: http://www.fda. gov/downloads/Drugs/DevelopmentApprovalProcess/HowDrugsareDevelopedandApproved/DrugandBiologicApprovalReports/INDActivityReports/UCM430188.pdf
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