Enzyme replacement therapy for congenital hypophosphatasia allows for surgical treatment of related complex craniosynostosis: A case series

Neurosurgical Focus

Volumn 38, Issue 5, 2015, Pages

  Kosnik Infinger, Libby ^a   Gendron, Craig ^a   Gordon, Christopher B ^a   Pan, Brian S ^a   van Aalst, John A ^a   Vogel, Timothy W ^a  

^a CINCINNATI CHILDREN'S HOSPITAL MEDICAL CENTER   (United States)

Author keywords

Asfotase alfa; Craniofacial; Craniosynostosis; ENB 0040; HPP; Hypophosphatasia; Pediatrics

Indexed keywords

ALKALINE PHOSPHATASE; ASFOTASE ALFA; HYBRID PROTEIN; IMMUNOGLOBULIN G;

CASE REPORT; CRANIOSYNOSTOSES; ENZYME REPLACEMENT; FEMALE; HUMAN; HYPOPHOSPHATASIA; MALE; POSTOPERATIVE CARE; PRESCHOOL CHILD; PROCEDURES; TREATMENT OUTCOME;

ALKALINE PHOSPHATASE; CHILD, PRESCHOOL; CRANIOSYNOSTOSES; ENZYME REPLACEMENT THERAPY; FEMALE; HUMANS; HYPOPHOSPHATASIA; IMMUNOGLOBULIN G; MALE; POSTOPERATIVE CARE; RECOMBINANT FUSION PROTEINS; TREATMENT OUTCOME;

EID: 84929628866     PISSN: None     EISSN: 10920684     Source Type: Journal    
DOI: 10.3171/2015.2.FOCUS14847     Document Type: Article

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