Principles for consistent value assessment and sustainable funding of orphan drugs in Europe

Orphanet Journal of Rare Diseases

Volumn 10, Issue 1, 2015, Pages

  Gutierrez, Laura ^a   Patris, Julien ^b   Hutchings, Adam ^c   Cowell, Warren ^d  

^a Celgene International   (Switzerland)

^b Celgene Bvba sarl Parc de l'Alliance   (Belgium)

^c Dolon Ltd   (United Kingdom)

^d Celgene Ltd   (United Kingdom)

Author keywords

Orphan medicinal products; Rare diseases; Value assessment

Indexed keywords

ORPHAN DRUG;

ARTICLE; AUTHORITY; BUDGET; CONSENSUS; DECISION MAKING; EUROPE; EUROPEAN UNION; EVIDENCE BASED PRACTICE; FUNDING; HEALTH CARE ACCESS; HEALTH CARE POLICY; HUMAN; INDUSTRY; LIFE EXPECTANCY; PHYSICIAN; PROGRAM SUSTAINABILITY; QUALITY CONTROL; RARE DISEASE; REIMBURSEMENT; REWARD; DRUG COST; DRUG MANUFACTURE; ECONOMICS; LEGISLATION AND JURISPRUDENCE; RARE DISEASES;

DRUG COSTS; EUROPE; HEALTH POLICY; HUMANS; ORPHAN DRUG PRODUCTION; RARE DISEASES;

EID: 84929324394     PISSN: None     EISSN: 17501172     Source Type: Journal    
DOI: 10.1186/s13023-015-0269-y     Document Type: Article

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