No effect of bezafibrate in patients with CPTII and VLCAD deficiencies

Journal of Inherited Metabolic Disease

Volumn 38, Issue 2, 2015, Pages 373-374

  Ørngreen, Mette Cathrine ^a   Vissing, John ^a   Laforét, Pascal ^b  

^a UNIVERSITY OF COPENHAGEN   (Denmark)

^b ASSISTANCE PUBLIQUE HÔPITAUX DE PARIS   (France)

Author keywords

[No Author keywords available]

Indexed keywords

BEZAFIBRATE; CARNITINE PALMITOYLTRANSFERASE; CARNITINE PALMITOYLTRANSFERASE II; LONG CHAIN ACYL COENZYME A DEHYDROGENASE; PLACEBO; UNCLASSIFIED DRUG; FATTY ACID;

CARNITINE PALMITOYLTRANSFERASE II DEFICIENCY; CONTROLLED STUDY; DOUBLE BLIND PROCEDURE; ENZYME DEFICIENCY; EXERCISE TOLERANCE; FATTY ACID OXIDATION; HEART RATE; HUMAN; HYPERINSULINEMIA; LETTER; LONG CHAIN ACYL COENZYME A DEHYDROGENASE DEFICIENCY; MUSCLE WEAKNESS; MYALGIA; MYOBLAST; MYOGLOBINURIA; RANDOMIZED CONTROLLED TRIAL; RHABDOMYOLYSIS; DEFICIENCY; DRUG EFFECTS; LIPID METABOLISM, INBORN ERRORS; LIPOLYSIS; METABOLISM; METABOLISM, INBORN ERRORS; MITOCHONDRIAL DISEASES; MUSCULAR DISEASES;

ACYL-COA DEHYDROGENASE, LONG-CHAIN; BEZAFIBRATE; CARNITINE O-PALMITOYLTRANSFERASE; FATTY ACIDS; HUMANS; LIPID METABOLISM, INBORN ERRORS; LIPOLYSIS; METABOLISM, INBORN ERRORS; MITOCHONDRIAL DISEASES; MUSCULAR DISEASES;

EID: 84925537681     PISSN: 01418955     EISSN: 15732665     Source Type: Journal    
DOI: 10.1007/s10545-014-9779-3     Document Type: Letter

References (6)

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