A proposed definition of rare diseases for China: From the perspective of return on investment in new orphan drugs

Orphanet Journal of Rare Diseases

Volumn 10, Issue 1, 2015, Pages

  Cui, Yazhou ^a   Han, Jinxiang ^a  

^a BEIJING HOSPITAL   (China)

Author keywords

China; Definition; Orphan drug; Rare diseases

Indexed keywords

ORPHAN DRUG;

ARTICLE; CHINA; DRUG COST; DRUG INDUSTRY; DRUG LEGISLATION; DRUG RESEARCH; HEALTH CARE SYSTEM; HUMAN; PREVALENCE; RARE DISEASE; CLASSIFICATION; DRUG APPROVAL; DRUG MANUFACTURE; ECONOMICS;

DRUG APPROVAL; HUMANS; ORPHAN DRUG PRODUCTION; RARE DISEASES;

EID: 84925442521     PISSN: None     EISSN: 17501172     Source Type: Journal    
DOI: 10.1186/s13023-015-0241-x     Document Type: Article

References (8)

1. Melnikova I. Rare diseases and orphan drugs. Nat Rev Drug Discov. 2012;11:267-8.
2. Shi Q, Gao C, Zhou W, Zhang BY, Chen JM, Tian C, et al. Surveillance for Creutzfeldt-Jakob disease in China from 2006 to 2007. BMC Public Health. 2008;8:360.
3. Wu JC, Liu L, Chen YC, Huang WC, Chen TJ, Cheng H. Ossification of the posterior longitudinal ligament in the cervical spine: an 11-year comprehensive national epidemiology study. Neurosurg Focus. 2011;30:E5.
4. Tambuyzer E. Rare diseases, orphan drugs and their regulation: questions and misconceptions. Nat Rev Drug Discov. 2010;9:921-9.
5. Song P, Gao J, Inagaki Y, Kokudo N, Tang W. Rare diseases, orphan drugs, and their regulation in Asia: current status and future perspectives. Intractable Rare Dis Res. 2012;1:3-9.
6. Aronson JK. Rare diseases and orphan drugs. Br J Clin Pharmacol. 2006;61:243-5.
7. JZMed. Innovative Drug R&D in China (Second Edition) - New Developments and Future Prospect. January. 2014. http://ep.yimg.com/ty/cdn/yhst-73374555502785/rndchina2ndtotal.pdf.pdf.
8. Qi J, Wang Q, Yu Z, Chen X, Wang F. Innovative drug R&D in China. Nat Rev Drug Discov. 2011;10:333-4.