Sporadic late-onset nemaline myopathy with MGUS; Long-term follow-up after melphalan and SCT

Neurology

Volumn 83, Issue 23, 2014, Pages 2133-2139

  Voermans, Nicol C ^a   Benveniste, Olivier ^b   Minnema, Monique C ^c   Lokhorst, Henk ^c   Lammens, Martin ^a,d   Meersseman, Wouter ^e   Delforge, Michel ^e   Kuntzer, Thierry ^f   Novy, Jan ^f   Pabst, Thomas ^g   Bouhour, Françoise ^h   Romero, Norma ^b   Leblond, Veronique ^b,i   Van Den Bergh, Peter ^b,i   Vekemans, Marie Christiane ^j   Van Engelen, Baziel G ^a   Eymard, Bruno ^b  

^a RADBOUD UNIVERSITY MEDICAL CENTER   (Netherlands)

^b PITIÉ SALPÊTRIÈRE HOSPITAL   (France)

^c UNIVERSITY MEDICAL CENTER UTRECHT   (Netherlands)

^d ANTWERP UNIVERSITY HOSPITAL   (Belgium)

^e UNIVERSITY HOSPITALS LEUVEN   (Belgium)

^f LAUSANNE UNIVERSITY HOSPITAL   (Switzerland)

^g UNIVERSITY OF BERN   (Switzerland)

^h Bron University Hospital Center   (France)

ⁱ Department of Neurology Neuromuscular Reference Centre   (France)

^j CLINIQUES UNIVERSITAIRES SAINT LUC   (Belgium)

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Author keywords

[No Author keywords available]

Indexed keywords

LENALIDOMIDE; MELPHALAN;

ADULT; ARTICLE; AUTOLOGOUS HEMATOPOIETIC STEM CELL TRANSPLANTATION; CASE STUDY; CLINICAL ARTICLE; DISEASE COURSE; DISEASE SEVERITY; DRUG MEGADOSE; ELECTRON MICROSCOPY; FEMALE; FOLLOW UP; HUMAN; HUMAN TISSUE; LONG TERM CARE; MALE; MIDDLE AGED; MONOCLONAL IMMUNOGLOBULINEMIA; MUSCLE STRENGTH; MUSCLE WEAKNESS; NEMALINE MYOPATHY; ONSET AGE; OUTCOME ASSESSMENT; PRIORITY JOURNAL; QUADRICEPS FEMORIS MUSCLE; RETROSPECTIVE STUDY; SPORADIC LATE ONSET NEMALINE MYOPATHY; SURVIVAL; THERAPY EFFECT; AUTOTRANSPLANTATION; COMPLICATION; MYOPATHIES, NEMALINE; PARAPROTEINEMIAS; PROCEDURES; STEM CELL TRANSPLANTATION; TREATMENT OUTCOME;

ADULT; AGE OF ONSET; FEMALE; FOLLOW-UP STUDIES; HUMANS; MALE; MELPHALAN; MYOPATHIES, NEMALINE; PARAPROTEINEMIAS; RETROSPECTIVE STUDIES; STEM CELL TRANSPLANTATION; TRANSPLANTATION, AUTOLOGOUS; TREATMENT OUTCOME;

EID: 84925282792     PISSN: 00283878     EISSN: 1526632X     Source Type: Journal    
DOI: 10.1212/WNL.0000000000001047     Document Type: Article

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