Patient-specific induced pluripotent stem cells (iPSCs) for the study and treatment of retinal degenerative diseases

Progress in Retinal and Eye Research

Volumn 44, Issue , 2015, Pages 15-35

  Wiley, Luke A ^a   Burnight, Erin R ^a   Songstad, Allison E ^a   Drack, Arlene V ^a   Mullins, Robert F ^a   Stone, Edwin M ^a,b   Tucker, Budd A ^a  

^a UNIVERSITY OF IOWA   (United States)

^b UNIVERSITY OF IOWA   (United States)

Author keywords

Cell transplantation; CRISPR based genome editing; Gene therapy; Induced pluripotent stem cells; Retinal degeneration

Indexed keywords

MALE GERM CELL ASSOCIATED KINASE; PHOSPHOTRANSFERASE; UNCLASSIFIED DRUG;

AGE RELATED MACULAR DEGENERATION; DRUG RESEARCH; EMBRYONIC STEM CELL; GENE AUGMENTATION; GENE THERAPY; HUMAN; IMMUNE SYSTEM; LEBER CONGENITAL AMAUROSIS; MENDELIAN RETINAL DISEASE; NEURONAL CEROID LIPOFUSCINOSIS; PLURIPOTENT STEM CELL; RETINA DEGENERATION; RETINA DISEASE; RETINITIS PIGMENTOSA; REVIEW; STEM CELL TRANSPLANTATION; TOTIPOTENT STEM CELL; USHER SYNDROME; VITELLIFORM MACULAR DEGENERATION; ANIMAL; DISEASE MODEL; GENETICS; MUTATION; RETINAL DEGENERATION; TRANSPLANTATION;

ANIMALS; DISEASE MODELS, ANIMAL; HUMANS; INDUCED PLURIPOTENT STEM CELLS; MUTATION; RETINAL DEGENERATION;

EID: 84916198284     PISSN: 13509462     EISSN: 18731635     Source Type: Journal    
DOI: 10.1016/j.preteyeres.2014.10.002     Document Type: Review

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