Pharmacologic rescue of an enzyme-trafficking defect in primary hyperoxaluria 1

Proceedings of the National Academy of Sciences of the United States of America

Volumn 111, Issue 40, 2014, Pages 14406-14411

  Miyata, Non ^a   Steffen, Janos ^a   Johnson, Meghan E ^a   Fargue, Sonia ^b,e   Danpure, Christopher J ^b   Koehler, Carla M ^a,c,d  

^a Department of Chemistry and Biochemistry ^*  (United States)

^b UNIVERSITY COLLEGE LONDON   (United Kingdom)

^c UNIVERSITY OF CALIFORNIA   (United States)

^d UNIVERSITY OF CALIFORNIA   (United States)

^e Alabama   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ALANINE-GLYOXYLATE TRANSAMINASE; AMINOTRANSFERASE; DEQUALINIUM; OXALIC ACID DERIVATIVE; PYRIDOXINE; TOPICAL ANTIINFECTIVE AGENT;

ANIMAL; CHO CELL LINE; CRICETULUS; DRUG EFFECTS; EMBRYOLOGY; FLUORESCENCE MICROSCOPY; GENETICS; HAMSTER; HUMAN; HYPEROXALURIA, PRIMARY; IMMUNOBLOTTING; METABOLISM; MITOCHONDRION; MUTATION; NONMAMMALIAN EMBRYO; PEROXISOME; PRECLINICAL STUDY; PROCEDURES; PROTEIN TRANSPORT; ZEBRA FISH;

ANIMALS; ANTI-INFECTIVE AGENTS, LOCAL; CHO CELLS; CRICETINAE; CRICETULUS; DEQUALINIUM; DRUG EVALUATION, PRECLINICAL; EMBRYO, NONMAMMALIAN; HUMANS; HYPEROXALURIA, PRIMARY; IMMUNOBLOTTING; MICROSCOPY, FLUORESCENCE; MITOCHONDRIA; MUTATION; OXALATES; PEROXISOMES; PROTEIN TRANSPORT; PYRIDOXINE; TRANSAMINASES; ZEBRAFISH;

EID: 84907707462     PISSN: 00278424     EISSN: 10916490     Source Type: Journal    
DOI: 10.1073/pnas.1408401111     Document Type: Article

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