Nicotinamide in Friedreich's ataxia: Useful or not?

The Lancet

Volumn 384, Issue 9942, 2014, Pages 474-475

  Lynch, David R ^a   Fischbeck, Kenneth H ^b  

^a CHILDREN S HOSPITAL OF PHILADELPHIA   (United States)

^b NATIONAL INSTITUTE OF NEUROLOGICAL DISORDERS AND STROKE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

FRATAXIN; HISTONE DEACETYLASE INHIBITOR; NICOTINAMIDE; HISTONE DEACETYLASE; MESSENGER RNA;

AMINO ACID SEQUENCE; CELL CULTURE; CHROMATIN STRUCTURE; DEACETYLATION; DISEASE SEVERITY; DORSAL ROOT; EPIGENETICS; FRATAXIN GENE; FRIEDREICH ATAXIA; GENE; GENE EXPRESSION; GENE SILENCING; GENETIC TRANSCRIPTION; HEART; HETEROCHROMATIN; HUMAN; INTRON; LONG TERM CARE; NAUSEA AND VOMITING; NONHUMAN; NOTE; PERIPHERAL BLOOD MONONUCLEAR CELL; PRIORITY JOURNAL; TREATMENT DURATION; UPREGULATION; CARDIOMYOPATHY; CLINICAL FEATURE; DRUG DOSE ESCALATION; NAUSEA; OPEN STUDY; PHASE 1 CLINICAL TRIAL (TOPIC); PHASE 2 CLINICAL TRIAL (TOPIC); PHASE 3 CLINICAL TRIAL (TOPIC); RANDOMIZED CONTROLLED TRIAL (TOPIC); SCOLIOSIS; SINGLE DRUG DOSE; VOMITING;

FEMALE; FRIEDREICH ATAXIA; HUMANS; IRON-BINDING PROTEINS; MALE; NIACINAMIDE; VITAMIN B COMPLEX;

EID: 84906318602     PISSN: 01406736     EISSN: 1474547X     Source Type: Journal    
DOI: 10.1016/S0140-6736(14)60573-0     Document Type: Note

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