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Volumn 20, Issue 5, 2014, Pages 476-477

CRISPR technology for gene therapy
[No Author Info available]

Author keywords

[No Author keywords available]

Indexed keywords

ARTICLE; BODY WEIGHT LOSS; CELL EXPANSION; CRISPR-CAS9 SYSTEM; DNA REPAIR; GENE EDITING; GENE THERAPY; HUMAN; HYDRODYNAMICS; NONHUMAN; PRIORITY JOURNAL; TYROSINEMIA; ANIMAL; CLUSTERED REGULARLY INTERSPACED SHORT PALINDROMIC REPEAT; GENETICS; METHODOLOGY; NOTE;

EID: 84904762304     PISSN: 10788956     EISSN: 1546170X     Source Type: Journal    
DOI: 10.1038/nm.3566     Document Type: Article
Times cited : (17)

References (12)
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  • 2
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  • 4
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  • 6
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    • Correction of a genetic disease in mouse via use of CRISPR-Cas9
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    • Wu, Y. et al. Correction of a genetic disease in mouse via use of CRISPR-Cas9. Cell Stem Cell 13, 659–662 (2013).
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  • 7
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  • 9
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