Successful RAG1-SCID gene therapy depends on the level of RAG1 expression

Journal of Allergy and Clinical Immunology

Volumn 134, Issue 1, 2014, Pages 242-243

  Pike Overzet, Karin ^a   Baum, Christopher ^b   Bredius, Robbert G M ^a   Cavazzana, Marina ^c   Driessen, Gert Jan ^d   Fibbe, Willem E ^a   Gaspar, H Bobby ^e   Hoeben, Rob C ^a   Lagresle Peyrou, Chantal ^c   Lankester, Arjan ^a   Meij, Pauline ^a   Schambach, Axel ^b   Thrasher, Adrian ^e   Van Dongen, Jacques J M ^d   Zwaginga, Jaap Jan ^a   Staal, Frank J T ^a  

^a LEIDEN UNIVERSITY MEDICAL CENTER   (Netherlands)

^b HANNOVER MEDICAL SCHOOL   (Germany)

^c HÔPITAL NECKER ENFANTS MALADES   (France)

^d ERASMUS MEDICAL CENTER   (Netherlands)

^e UNIVERSITY COLLEGE LONDON   (United Kingdom)

Author keywords

[No Author keywords available]

Indexed keywords

LENTIVIRUS VECTOR; RAG1 PROTEIN; HOMEODOMAIN PROTEIN;

GENE THERAPY; HUMAN; LETTER; NONHUMAN; PRIORITY JOURNAL; PROTEIN EXPRESSION; THYMUS; ANIMAL; FEMALE; GENE VECTOR; GENETICS; LENTIVIRINAE; MALE; SEVERE COMBINED IMMUNODEFICIENCY;

ANIMALS; FEMALE; GENETIC THERAPY; GENETIC VECTORS; HOMEODOMAIN PROTEINS; HUMANS; LENTIVIRUS; MALE; SEVERE COMBINED IMMUNODEFICIENCY;

EID: 84903635356     PISSN: 00916749     EISSN: 10976825     Source Type: Journal    
DOI: 10.1016/j.jaci.2014.04.033     Document Type: Letter

References (7)

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