A survey of breakthrough therapy designations

Nature Biotechnology

Volumn 32, Issue 4, 2014, Pages 323-330

  Aggarwal, Saurabh Rob ^a,b  

^a Novel Health Strategies LLC   (United States)

^b Institute for Women's Policy Research   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

DRUG THERAPY;

HEPATITIS C;

DISEASE CONTROL;

3,4 DIAMINOPYRIDINE; ABT 450; ALECTINIB; ANDEXANET ALFA; ASFOTASE ALFA; ASUNAPREVIR; BECLABUVIR; BIMAGRUMAB; CERITINIB; DACLATASVIR; DARATUMUMAB; DASABUVIR; DRISAPERSEN; ENTINOSTAT; IBRUTINIB; IDELALISIB; IVACAFTOR; LEDIPASVIR; LUMACAFTOR; OBINUTUZUMAB; OFATUMUMAB; OMBITASVIR; PALBOCICLIB; PEMBROLIZUMAB; SEBELIPASE ALFA; SERELAXIN; SOFOSBUVIR; TAFENOQUINE; UNINDEXED DRUG; VOLASERTIB; NEW DRUG;

ACUTE GRANULOCYTIC LEUKEMIA; ACUTE HEART FAILURE; ADVANCED CANCER; ANTIVIRAL THERAPY; ARTICLE; BLEEDING DISORDER; BREAKTHROUGH THERAPY DESIGNATION; BREAST CANCER; CANCER CHEMOTHERAPY; CANCER RECURRENCE; CHRONIC LYMPHATIC LEUKEMIA; CYSTIC FIBROSIS; DRUG APPROVAL; DUCHENNE MUSCULAR DYSTROPHY; EATON LAMBERT SYNDROME; FOOD AND DRUG ADMINISTRATION; HEALTH SURVEY; HEPATITIS C; HUMAN; HYPOPHOSPHATASIA; INCLUSION BODY MYOSITIS; LUNG NON SMALL CELL CANCER; LYSOSOMAL ACID LIPASE DEFICIENCY; LYSOSOME STORAGE DISEASE; MALARIA; MANTLE CELL LYMPHOMA; MEDICATION THERAPY MANAGEMENT; MELANOMA; MULTICENTER STUDY (TOPIC); MULTIPLE MYELOMA; PHASE 1 CLINICAL TRIAL (TOPIC); PHASE 2 CLINICAL TRIAL (TOPIC); PHASE 3 CLINICAL TRIAL (TOPIC); PRIORITY JOURNAL; RANDOMIZED CONTROLLED TRIAL (TOPIC); UNITED STATES; WALDENSTROEM MACROGLOBULINEMIA; DRUG INDUSTRY; LEGISLATION AND JURISPRUDENCE; PROCEDURES; TIME;

DRUG APPROVAL; DRUG INDUSTRY; DRUGS, INVESTIGATIONAL; TIME FACTORS; UNITED STATES; UNITED STATES FOOD AND DRUG ADMINISTRATION;

EID: 84900859536     PISSN: 10870156     EISSN: 15461696     Source Type: Journal    
DOI: 10.1038/nbt.2864     Document Type: Article

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