-
1
-
-
0001142644
-
Parvoviridae: The viruses and their replication
-
Muzyczka N, Berns K (2001) Parvoviridae: the viruses and their replication. Fields virology 2: 2327-2359.
-
(2001)
Fields Virology
, vol.2
, pp. 2327-2359
-
-
Muzyczka, N.1
Berns, K.2
-
2
-
-
0029898764
-
A phase I study of an adeno-associated Virus-CFTR gene vector in adult CF patients with mild lung disease
-
Flotte T, Carter B, Conrad C, Guggino W, Reynolds T, et al. (1996) A phase I study of an adeno-associated virus-CFTR gene vector in adult CF patients with mild lung disease. Hum Gene Ther 7: 1145-1159. (Pubitemid 26202733)
-
(1996)
Human Gene Therapy
, vol.7
, Issue.9
, pp. 1145-1159
-
-
Flotte, T.1
Carter, B.2
Conrad, C.3
Guggino, W.4
Reynolds, T.5
Rosenstein, B.6
Taylor, G.7
Walden, S.8
Wetzel, R.9
-
3
-
-
44249085878
-
Safety and efficacy of gene transfer for Leber's congenital amaurosis
-
DOI 10.1056/NEJMoa0802315
-
Maguire AM, Simonelli F, Pierce EA, Pugh EN Jr, Mingozzi F, et al. (2008) Safety and efficacy of gene transfer for Leber's congenital amaurosis. N Engl J Med 358: 2240-2248. (Pubitemid 351724453)
-
(2008)
New England Journal of Medicine
, vol.358
, Issue.21
, pp. 2240-2248
-
-
Maguire, A.M.1
Simonelli, F.2
Pierce, E.A.3
Pugh Jr., E.N.4
Mingozzi, F.5
Bennicelli, J.6
Banfi, S.7
Marshall, K.A.8
Testa, F.9
Surace, E.M.10
Rossi, S.11
Lyubarsky, A.12
Arruda, V.R.13
Konkle, B.14
Stone, E.15
Sun, J.16
Jacobs, J.17
Dell'Osso, L.18
Hertle, R.19
Ma, J.-X.20
Redmond, T.M.21
Zhu, X.22
Hauck, B.23
Zelenaia, O.24
Shindler, K.S.25
Maguire, M.G.26
Wright, J.F.27
Volpe, N.J.28
McDonnell, J.W.29
Auricchio, A.30
High, K.A.31
Bennett, J.32
more..
-
4
-
-
33644820684
-
Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response
-
DOI 10.1038/nm1358, PII N1358
-
Manno CS, Pierce GF, Arruda VR, Glader B, Ragni M, et al. (2006) Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response. Nat Med 12: 342-347. (Pubitemid 43355084)
-
(2006)
Nature Medicine
, vol.12
, Issue.3
, pp. 342-347
-
-
Manno, C.S.1
Arruda, V.R.2
Pierce, G.F.3
Glader, B.4
Ragni, M.5
Rasko, J.6
Ozelo, M.C.7
Hoots, K.8
Blatt, P.9
Konkle, B.10
Dake, M.11
Kaye, R.12
Razavi, M.13
Zajko, A.14
Zehnder, J.15
Nakai, H.16
Chew, A.17
Leonard, D.18
Wright, J.F.19
Lessard, R.R.20
Sommer, J.M.21
Tigges, M.22
Sabatino, D.23
Luk, A.24
Jiang, H.25
Mingozzi, F.26
Couto, L.27
Ertl, H.C.28
High, K.A.29
Kay, M.A.30
more..
-
5
-
-
84855161388
-
Adenovirus-associated virus vector-mediated gene transfer in hemophilia B
-
Nathwani AC, Tuddenham EG, Rangarajan S, Rosales C, McIntosh J, et al. (2011) Adenovirus-associated virus vector-mediated gene transfer in hemophilia B. N Engl J Med 365: 2357-2365.
-
(2011)
N Engl J Med
, vol.365
, pp. 2357-2365
-
-
Nathwani, A.C.1
Tuddenham, E.G.2
Rangarajan, S.3
Rosales, C.4
McIntosh, J.5
-
6
-
-
84255199681
-
Production of recombinant adeno-associated viral vectors and use in in vitro and in vivo administration
-
Chapter 4: Unit 4 17
-
Gray SJ, Choi VW, Asokan A, Haberman RA, McCown TJ, et al. (2011) Production of recombinant adeno-associated viral vectors and use in in vitro and in vivo administration. Curr Protoc Neurosci Chapter 4: Unit 4 17.
-
(2011)
Curr Protoc Neurosci
-
-
Gray, S.J.1
Choi, V.W.2
Asokan, A.3
Haberman, R.A.4
McCown, T.J.5
-
7
-
-
34347252689
-
Production and characterization of adeno-associated viral vectors
-
Grieger JC, Choi VW, Samulski RJ (2006) Production and characterization of adeno-associated viral vectors. Nat Protoc 1: 1412-1428.
-
(2006)
Nat Protoc
, vol.1
, pp. 1412-1428
-
-
Grieger, J.C.1
Choi, V.W.2
Samulski, R.J.3
-
8
-
-
79955405275
-
Good manufacturing practice production of self-complementary serotype 8 adeno-associated viral vector for a hemophilia B clinical trial
-
Allay JA, Sleep S, Long S, Tillman DM, Clark R, et al. (2011) Good manufacturing practice production of self-complementary serotype 8 adeno-associated viral vector for a hemophilia B clinical trial. Hum Gene Ther 22: 595-604.
-
(2011)
Hum Gene Ther
, vol.22
, pp. 595-604
-
-
Allay, J.A.1
Sleep, S.2
Long, S.3
Tillman, D.M.4
Clark, R.5
-
9
-
-
84872030621
-
Analysis of particle content of recombinant adeno-associated virus serotype 8 vectors by ion-exchange chromatography
-
Lock M, Alvira MR, Wilson JM (2012) Analysis of particle content of recombinant adeno-associated virus serotype 8 vectors by ion-exchange chromatography. Hum Gene Ther Methods 23: 56-64.
-
(2012)
Hum Gene Ther Methods
, vol.23
, pp. 56-64
-
-
Lock, M.1
Alvira, M.R.2
Wilson, J.M.3
-
10
-
-
68949202566
-
Transient transfection methods for clinical adeno-associated viral vector production
-
Wright JF (2009) Transient transfection methods for clinical adeno-associated viral vector production. Hum Gene Ther 20: 698-706.
-
(2009)
Hum Gene Ther
, vol.20
, pp. 698-706
-
-
Wright, J.F.1
-
11
-
-
77950858020
-
High AAV vector purity results in serotype- and tissue-independent enhancement of transduction efficiency
-
Ayuso E, Mingozzi F, Montane J, Leon X, Anguela XM, et al. (2010) High AAV vector purity results in serotype- and tissue-independent enhancement of transduction efficiency. Gene Ther 17: 503-510.
-
(2010)
Gene Ther
, vol.17
, pp. 503-510
-
-
Ayuso, E.1
Mingozzi, F.2
Montane, J.3
Leon, X.4
Anguela, X.M.5
-
12
-
-
80051993162
-
Adeno-associated viral vector manufacturing: Keeping pace with accelerating clinical development
-
Wright JF (2011) Adeno-associated viral vector manufacturing: keeping pace with accelerating clinical development. Hum Gene Ther 22: 913-914.
-
(2011)
Hum Gene Ther
, vol.22
, pp. 913-914
-
-
Wright, J.F.1
-
13
-
-
33744937902
-
Characterization of the capsid protein glycosylation of adeno-associated virus type 2 by high-resolution mass spectrometry
-
DOI 10.1128/JVI.02417-05
-
Murray S, Nilsson CL, Hare JT, Emmett MR, Korostelev A, et al. (2006) Characterization of the capsid protein glycosylation of adeno-associated virus type 2 by high-resolution mass spectrometry. J Virol 80: 6171-6176. (Pubitemid 43849195)
-
(2006)
Journal of Virology
, vol.80
, Issue.12
, pp. 6171-6176
-
-
Murray, S.1
Nilsson, C.L.2
Hare, J.T.3
Emmett, M.R.4
Korostelev, A.5
Ongley, H.6
Marshall, A.G.7
Chapman, M.S.8
-
14
-
-
58149376502
-
Identification of cellular proteins that interact with the adeno-associated virus rep protein
-
Nash K, Chen W, Salganik M, Muzyczka N (2009) Identification of cellular proteins that interact with the adeno-associated virus rep protein. J Virol 83: 454-469.
-
(2009)
J Virol
, vol.83
, pp. 454-469
-
-
Nash, K.1
Chen, W.2
Salganik, M.3
Muzyczka, N.4
-
15
-
-
67349159102
-
Adeno-associated virus capsid serotype identification: Analytical methods development and application
-
Van Vliet K, Mohiuddin Y, McClung S, Blouin V, Rolling F, et al. (2009) Adeno-associated virus capsid serotype identification: Analytical methods development and application. J Virol Methods 159: 167-177.
-
(2009)
J Virol Methods
, vol.159
, pp. 167-177
-
-
Van Vliet, K.1
Mohiuddin, Y.2
McClung, S.3
Blouin, V.4
Rolling, F.5
-
16
-
-
34548761857
-
Existence of transient functional double-stranded DNA intermediates during recombinant AAV transduction
-
DOI 10.1073/pnas.0702778104
-
Wang J, Xie J, Lu H, Chen L, Hauck B, et al. (2007) Existence of transient functional double-stranded DNA intermediates during recombinant AAV transduction. Proc Natl Acad Sci U S A 104: 13104-13109. (Pubitemid 351737600)
-
(2007)
Proceedings of the National Academy of Sciences of the United States of America
, vol.104
, Issue.32
, pp. 13104-13109
-
-
Wang, J.1
Xie, J.2
Lu, H.3
Chen, L.4
Hauck, B.5
Samulski, R.J.6
Xiao, W.7
-
17
-
-
62749167014
-
Enhancement of adeno-associated virus infection by mobilizing capsids into and out of the nucleolus
-
Johnson JS, Samulski RJ (2009) Enhancement of adeno-associated virus infection by mobilizing capsids into and out of the nucleolus. J Virol 83: 2632-2644.
-
(2009)
J Virol
, vol.83
, pp. 2632-2644
-
-
Johnson, J.S.1
Samulski, R.J.2
-
18
-
-
0033541943
-
A 110-kDa nuclear shuttle protein, nucleolin, specifically binds to adeno-associated virus type 2 (AAV-2) capsid
-
DOI 10.1006/viro.1999.9664
-
Qiu J, Brown KE (1999) A 110-kDa nuclear shuttle protein, nucleolin, specifically binds to adeno-associated virus type 2 (AAV-2) capsid. Virology 257: 373-382. (Pubitemid 29393405)
-
(1999)
Virology
, vol.257
, Issue.2
, pp. 373-382
-
-
Qiu, J.1
Brown, K.E.2
-
19
-
-
33751414730
-
Adeno-associated virus interactions with B23/Nucleophosmin: Identification of sub-nucleolar virion regions
-
DOI 10.1016/j.virol.2006.07.050, PII S0042682206005095
-
Bevington JM, Needham PG, Verrill KC, Collaco RF, Basrur V, et al. (2007) Adeno-associated virus interactions with B23/Nucleophosmin: identification of sub-nucleolar virion regions. Virology 357: 102-113. (Pubitemid 44820332)
-
(2007)
Virology
, vol.357
, Issue.1
, pp. 102-113
-
-
Bevington, J.M.1
Needham, P.G.2
Verrill, K.C.3
Collaco, R.F.4
Basrur, V.5
Trempe, J.P.6
-
20
-
-
0033799367
-
Endocytosis and nuclear trafficking of adeno-associated virus type 2 are controlled by rac1 and phosphatidylinositol-3 kinase activation
-
Sanlioglu S, Benson PK, Yang J, Atkinson EM, Reynolds T, et al. (2000) Endocytosis and nuclear trafficking of adeno-associated virus type 2 are controlled by rac1 and phosphatidylinositol-3 kinase activation. J Virol 74: 9184-9196.
-
(2000)
J Virol
, vol.74
, pp. 9184-9196
-
-
Sanlioglu, S.1
Benson, P.K.2
Yang, J.3
Atkinson, E.M.4
Reynolds, T.5
-
21
-
-
0035043237
-
Adeno-associated virus type 2-mediated gene transfer: Altered endocytic processing enhances transduction efficiency in murine fibroblasts
-
DOI 10.1128/JVI.75.9.4080-4090.2001
-
Hansen J, Qing K, Srivastava A (2001) Adeno-associated virus type 2-mediated gene transfer: altered endocytic processing enhances transduction efficiency in murine fibroblasts. J Virol 75: 4080-4090. (Pubitemid 32410120)
-
(2001)
Journal of Virology
, vol.75
, Issue.9
, pp. 4080-4090
-
-
Hansen, J.1
Qing, K.2
Srivastava, A.3
-
22
-
-
84861189907
-
High-efficiency transduction of human monocyte-derived dendritic cells by capsid-modified recombinant AAV2 vectors
-
Aslanidi GV, Rivers AE, Ortiz L, Govindasamy L, Ling C, et al. (2012) High-efficiency transduction of human monocyte-derived dendritic cells by capsid-modified recombinant AAV2 vectors. Vaccine 30: 3908-3917.
-
(2012)
Vaccine
, vol.30
, pp. 3908-3917
-
-
Aslanidi, G.V.1
Rivers, A.E.2
Ortiz, L.3
Govindasamy, L.4
Ling, C.5
-
23
-
-
54549096772
-
Tyrosine-phosphorylation of AAV2 vectors and its consequences on viral intracellular trafficking and transgene expression
-
Zhong L, Li B, Jayandharan G, Mah CS, Govindasamy L, et al. (2008) Tyrosine-phosphorylation of AAV2 vectors and its consequences on viral intracellular trafficking and transgene expression. Virology 381: 194-202.
-
(2008)
Virology
, vol.381
, pp. 194-202
-
-
Zhong, L.1
Li, B.2
Jayandharan, G.3
Mah, C.S.4
Govindasamy, L.5
-
24
-
-
45549090635
-
Next generation of adeno-associated virus 2 vectors: Point mutations in tyrosines lead to high-efficiency transduction at lower doses
-
DOI 10.1073/pnas.0802866105
-
Zhong L, Li B, Mah CS, Govindasamy L, Agbandje-McKenna M, et al. (2008) Next generation of adeno-associated virus 2 vectors: point mutations in tyrosines lead to high-efficiency transduction at lower doses. Proc Natl Acad Sci U S A 105: 7827-7832. (Pubitemid 351872723)
-
(2008)
Proceedings of the National Academy of Sciences of the United States of America
, vol.105
, Issue.22
, pp. 7827-7832
-
-
Zhong, L.1
Li, B.2
Mah, C.S.3
Govindasamy, L.4
Agbandje-McKenna, M.5
Cooper, M.6
Herzog, R.W.7
Zolotukhin, I.8
Warrington Jr., K.H.9
Weigel-Van, A.K.A.10
Hobbs, J.A.11
Zolotukhin, S.12
Muzyczka, N.13
Srivastava, A.14
-
25
-
-
51049086842
-
Strategies for improving the transduction efficiency of single-stranded adeno-associated virus vectors in vitro and in vivo
-
Jayandharan GR, Zhong L, Li B, Kachniarz B, Srivastava A (2008) Strategies for improving the transduction efficiency of single-stranded adeno-associated virus vectors in vitro and in vivo. Gene Ther 15: 1287-1293.
-
(2008)
Gene Ther
, vol.15
, pp. 1287-1293
-
-
Jayandharan, G.R.1
Zhong, L.2
Li, B.3
Kachniarz, B.4
Srivastava, A.5
-
26
-
-
0344628577
-
Impurity of recombinant adeno-associated virus type 2 affects the transduction characteristics following subretinal injection in the rat
-
DOI 10.1016/j.visres.2003.09.032
-
Shen WY, Lai YK, Lai CM, Rakoczy PE (2004) Impurity of recombinant adeno-associated virus type 2 affects the transduction characteristics following subretinal injection in the rat. Vision Res 44: 339-348. (Pubitemid 37501030)
-
(2004)
Vision Research
, vol.44
, Issue.4
, pp. 339-348
-
-
Shen, W.-Y.1
Lai, Y.K.Y.2
Lai, C.-M.3
Rakoczy, P.E.4
-
27
-
-
58149391424
-
Proteomic analysis of oxidative stress-responsive proteins in human pneumocytes: Insight into the regulation of DJ-1 expression
-
Duan X, Kelsen SG, Merali S (2008) Proteomic analysis of oxidative stress-responsive proteins in human pneumocytes: insight into the regulation of DJ-1 expression. J Proteome Res 7: 4955-4961.
-
(2008)
J Proteome Res
, vol.7
, pp. 4955-4961
-
-
Duan, X.1
Kelsen, S.G.2
Merali, S.3
-
28
-
-
77952969413
-
SILAC analysis of oxidative stress-mediated proteins in human pneumocytes: New role for treacle
-
Duan X, Kelsen SG, Clarkson AB Jr, Ji R, Merali S (2010) SILAC analysis of oxidative stress-mediated proteins in human pneumocytes: new role for treacle. Proteomics 10: 2165-2174.
-
(2010)
Proteomics
, vol.10
, pp. 2165-2174
-
-
Duan, X.1
Kelsen, S.G.2
Clarkson Jr., A.B.3
Ji, R.4
Merali, S.5
|