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Volumn 383, Issue 9915, 2014, Pages 436-448

Reduced-intensity conditioning and HLA-matched haemopoietic stem-cell transplantation in patients with chronic granulomatous disease: A prospective multicentre study

(34)  Güngör, Tayfun a   Teira, Pierre b   Slatter, Mary c   Stussi, Georg d   Stepensky, Polina e   Moshous, Despina f   Vermont, Clementien g   Ahmad, Imran h   Shaw, Peter J i   Da Cunha, José Marcos Telles j   Schlegel, Paul G k   Hough, Rachel l   Fasth, Anders m   Kentouche, Karim n   Gruhn, Bernd n   Fernandes, Juliana F o   Lachance, Silvy h   Bredius, Robbert g   Resnick, Igor B e   Belohradsky, Bernd H p   more..


Author keywords

[No Author keywords available]

Indexed keywords

ALEMTUZUMAB; BUSULFAN; CYCLOSPORIN A; FLUDARABINE; FLUORODEOXYGLUCOSE F 18; MYCOPHENOLIC ACID 2 MORPHOLINOETHYL ESTER; RITUXIMAB; TACROLIMUS; THYMOCYTE ANTIBODY; TREOSULFAN;

EID: 84895068883     PISSN: 01406736     EISSN: 1474547X     Source Type: Journal    
DOI: 10.1016/S0140-6736(13)62069-3     Document Type: Article
Times cited : (305)

References (32)
  • 1
    • 65349179624 scopus 로고    scopus 로고
    • Chronic granulomatous disease: The european experience
    • van den Berg JM, van Koppen E, Ahlin A, et al. Chronic granulomatous disease: the European experience. PLoS One 2009; 4: e5234.
    • (2009) PLoS One , vol.4
    • Van Den Berg, J.M.1    Van Koppen, E.2    Ahlin, A.3
  • 2
    • 0034040532 scopus 로고    scopus 로고
    • Chronic granulomatous disease. Report on a national registry of 368 patients
    • Winkelstein JA, Marino MC, Johnston RB Jr, et al Chronic granulomatous disease. Report on a national registry of 368 patients. Medicine (Baltimore) 2000; 79: 155-69.
    • (2000) Medicine (Baltimore) , vol.79 , pp. 155-169
    • Winkelstein, J.A.1    Marino, M.C.2    Johnston Jr., R.B.3
  • 3
    • 72849147215 scopus 로고    scopus 로고
    • Actinomyces in chronic granulomatous disease: An emerging and unanticipated pathogen
    • Reichenbach J, Lopatin U, Mahlaoui N., et al Actinomyces in chronic granulomatous disease: an emerging and unanticipated pathogen. Clin Infect Dis 2009; 49: 1703-10.
    • (2009) Clin Infect Dis , vol.49 , pp. 1703-1710
    • Reichenbach, J.1    Lopatin, U.2    Mahlaoui, N.3
  • 4
    • 79851510725 scopus 로고    scopus 로고
    • Advances in the diagnosis and treatment of chronic granulomatous disease
    • Seger RA. Advances in the diagnosis and treatment of chronic granulomatous disease. Curr Opin Hematol 2011; 18: 36-41.
    • (2011) Curr Opin Hematol , vol.18 , pp. 36-41
    • Seger, R.A.1
  • 5
    • 77956601381 scopus 로고    scopus 로고
    • Inflammasome activation in NADPH oxidase defective mononuclear phagocytes from patients with chronic granulomatous disease
    • Meissner F, Seger RA, Moshous D, Fischer A., Reichenbach J, Zychlinsky A. Inflammasome activation in NADPH oxidase defective mononuclear phagocytes from patients with chronic granulomatous disease. Blood 2010; 116: 1570-73.
    • (2010) Blood , vol.116 , pp. 1570-1573
    • Meissner, F.1    Seger, R.A.2    Moshous, D.3    Fischer, A.4    Reichenbach, J.5    Zychlinsky, A.6
  • 6
    • 84867573262 scopus 로고    scopus 로고
    • Hyperinflammation of chronic granulomatous disease is abolished by NOX2 reconstitution in macrophages and dendritic cells
    • Deffert C., Carnesecchi S, Yuan H., et al Hyperinflammation of chronic granulomatous disease is abolished by NOX2 reconstitution in macrophages and dendritic cells. J Pathol 2012; 228: 341-50.
    • (2012) J Pathol , vol.228 , pp. 341-350
    • Deffert, C.1    Carnesecchi, S.2    Yuan, H.3
  • 7
    • 77950359402 scopus 로고    scopus 로고
    • Therapeutic strategy in p47-phox deficient chronic granulomatous disease presenting as inflammatory bowel disease
    • Freudenberg F, Wintergerst U, Roesen-Wolff A, et al Therapeutic strategy in p47-phox deficient chronic granulomatous disease presenting as inflammatory bowel disease. J Allergy Clin Immunol 2010; 125: 943-46.
    • (2010) J Allergy Clin Immunol , vol.125 , pp. 943-946
    • Freudenberg, F.1    Wintergerst, U.2    Roesen-Wolff, A.3
  • 8
    • 78650918337 scopus 로고    scopus 로고
    • Residual NADPH oxidase and survival in chronic granulomatous disease
    • Kuhns DB, Alvord WG, Heller T, et al Residual NADPH oxidase and survival in chronic granulomatous disease. N Engl J Med 2010; 363: 2600-10.
    • (2010) N Engl J Med , vol.363 , pp. 2600-2610
    • Kuhns, D.B.1    Alvord, W.G.2    Heller, T.3
  • 9
    • 0017599399 scopus 로고
    • Bone-marrow transplant from an unrelated donor for chronic granulomatous disease
    • The Westminster Hospitals Bone-Marrow Transplant Team
    • The Westminster Hospitals Bone-Marrow Transplant Team. Bone-marrow transplant from an unrelated donor for chronic granulomatous disease. Lancet 1977; 309: 210-13.
    • (1977) Lancet , vol.309 , pp. 210-213
  • 10
    • 0037114622 scopus 로고    scopus 로고
    • Treatment of chronic granulomatous disease with myeloablative conditioning and an unmodified hemopoietic allograft: A survey of the european experience, 1985-2000
    • Seger RA, Gungor T, Belohradsky B.H., et al Treatment of chronic granulomatous disease with myeloablative conditioning and an unmodified hemopoietic allograft: a survey of the European experience, 1985-2000. Blood 2002; 100: 4344-50.
    • (2002) Blood , vol.100 , pp. 4344-4350
    • Seger, R.A.1    Gungor, T.2    Belohradsky, B.H.3
  • 11
    • 69849087669 scopus 로고    scopus 로고
    • Hematopoietic stem cell transplantation from matched unrelated donors in chronic granulomatous disease
    • Schuetz C, Hoenig M, Gatz S., et al Hematopoietic stem cell transplantation from matched unrelated donors in chronic granulomatous disease. Immunol Res 2009; 44: 35-41.
    • (2009) Immunol Res , vol.44 , pp. 35-41
    • Schuetz, C.1    Hoenig, M.2    Gatz, S.3
  • 12
    • 61949241213 scopus 로고    scopus 로고
    • Unrelated donor and HLA-identical sibling haematopoietic stem cell transplantation cure chronic granulomatous disease with good long-term outcome and growth
    • Soncini E, Slatter MA, Jones L.B., et al Unrelated donor and HLA-identical sibling haematopoietic stem cell transplantation cure chronic granulomatous disease with good long-term outcome and growth. Br J Haematol 2009; 145: 73-83.
    • (2009) Br J Haematol , vol.145 , pp. 73-83
    • Soncini, E.1    Slatter, M.A.2    Jones, L.B.3
  • 13
    • 75149126079 scopus 로고    scopus 로고
    • Successful hematopoietic stem-cell transplantation in a patient with chronic granulomatous disease and McLeod phenotype sensitized to kx and K antigens
    • Honig M, Flegel WA, Schwarz K, et al Successful hematopoietic stem-cell transplantation in a patient with chronic granulomatous disease and McLeod phenotype sensitized to Kx and K antigens. Bone Marrow Transplant 2010; 45: 209-11.
    • (2010) Bone Marrow Transplant , vol.45 , pp. 209-211
    • Honig, M.1    Flegel, W.A.2    Schwarz, K.3
  • 14
    • 84455205615 scopus 로고    scopus 로고
    • Excellent survival after sibling or unrelated donor stem cell transplantation for chronic granulomatous disease
    • Martinez CA, Shah S, Shearer W T, et al Excellent survival after sibling or unrelated donor stem cell transplantation for chronic granulomatous disease. J Allergy Clin Immunol 2012; 129: 176-83.
    • (2012) J Allergy Clin Immunol , vol.129 , pp. 176-183
    • Martinez, C.A.1    Shah, S.2    Shearer W, T.3
  • 15
    • 84865170098 scopus 로고    scopus 로고
    • Myeloablative transplantation using either cord blood or bone marrow leads to immune recovery, high long-term donor chimerism and excellent survival in chronic granulomatous disease
    • Tewari P, Martin PL, Mendizabal A, et al Myeloablative transplantation using either cord blood or bone marrow leads to immune recovery, high long-term donor chimerism and excellent survival in chronic granulomatous disease. Biol Blood Marrow Transplant 2012; 18: 1368-77.
    • (2012) Biol Blood Marrow Transplant , vol.18 , pp. 1368-1377
    • Tewari, P.1    Martin, P.L.2    Mendizabal, A.3
  • 16
    • 0035932520 scopus 로고    scopus 로고
    • Treatment of chronic granulomatous disease with nonmyeloablative conditioning and a T-cell-depleted hematopoietic allograft
    • Horwitz ME, Barrett AJ, Brown M.R., et al Treatment of chronic granulomatous disease with nonmyeloablative conditioning and a T-cell-depleted hematopoietic allograft. N Engl J Med 2001; 344: 881-88.
    • (2001) N Engl J Med , vol.344 , pp. 881-888
    • Horwitz, M.E.1    Barrett, A.J.2    Brown, M.R.3
  • 19
    • 34848829531 scopus 로고    scopus 로고
    • Prospective validation of a novel IV busulfan fixed dosing for paediatric patients to improve therapeutic AUC targeting without drug monitoring
    • Vassal G, Michel G, Esperou H., et al Prospective validation of a novel IV busulfan fixed dosing for paediatric patients to improve therapeutic AUC targeting without drug monitoring. Cancer Chemother Pharmacol 2008; 61: 113-23.
    • (2008) Cancer Chemother Pharmacol , vol.61 , pp. 113-123
    • Vassal, G.1    Michel, G.2    Esperou, H.3
  • 20
    • 80052087580 scopus 로고    scopus 로고
    • Therapeutic drug monitoring is essential for intravenous busulfan therapy in pediatric hematopoietic stem cell recipients
    • Malar R, Sjoo F, Rentsch K., Hassan M, Gungor T. Therapeutic drug monitoring is essential for intravenous busulfan therapy in pediatric hematopoietic stem cell recipients. Pediatric Transplantation 2011; 15: 580-88.
    • (2011) Pediatric Transplantation , vol.15 , pp. 580-588
    • Malar, R.1    Sjoo, F.2    Rentsch, K.3    Hassan, M.4    Gungor, T.5
  • 21
    • 37349060017 scopus 로고    scopus 로고
    • Once-daily intravenous busulfan with therapeutic drug monitoring compared to conventional oral busulfan improves survival and engraftment in children undergoing allogeneic stem cell transplantation
    • Bartelink IH, Bredius RG, Ververs T.T., et al Once-daily intravenous busulfan with therapeutic drug monitoring compared to conventional oral busulfan improves survival and engraftment in children undergoing allogeneic stem cell transplantation. Biol Blood Marrow Transplant 2008; 14: 88-98.
    • (2008) Biol Blood Marrow Transplant , vol.14 , pp. 88-98
    • Bartelink, I.H.1    Bredius, R.G.2    Ververs, T.T.3
  • 22
    • 0033768672 scopus 로고    scopus 로고
    • A phase I/II study of multiple-dose intravenous busulfan as myeloablation prior to stem cell transplantation
    • Olavarria E, Hassan M, Eades A., et al A phase I/II study of multiple-dose intravenous busulfan as myeloablation prior to stem cell transplantation. Leukemia 2000; 14: 1954-59.
    • (2000) Leukemia , vol.14 , pp. 1954-1959
    • Olavarria, E.1    Hassan, M.2    Eades, A.3
  • 23
    • 0032006125 scopus 로고    scopus 로고
    • Nonmyeloablative stem cell transplantation and cell therapy as an alternative to conventional bone marrow transplantation with lethal cytoreduction for the treatment of malignant and nonmalignant hematologic diseases
    • Slavin S, Nagler A, Naparstek E., et al Nonmyeloablative stem cell transplantation and cell therapy as an alternative to conventional bone marrow transplantation with lethal cytoreduction for the treatment of malignant and nonmalignant hematologic diseases. Blood 1998; 91: 756-63.
    • (1998) Blood , vol.91 , pp. 756-763
    • Slavin, S.1    Nagler, A.2    Naparstek, E.3
  • 24
    • 3042753988 scopus 로고    scopus 로고
    • Reduced intensity haemopoietic stem-cell transplantation for treatment of non-malignant diseases in children
    • Jacobsohn DA, Duerst R, Tse W., Kletzel M. Reduced intensity haemopoietic stem-cell transplantation for treatment of non-malignant diseases in children. Lancet 2004; 364: 156-62.
    • (2004) Lancet , vol.364 , pp. 156-162
    • Jacobsohn, D.A.1    Duerst, R.2    Tse, W.3    Kletzel, M.4
  • 25
    • 20544436474 scopus 로고    scopus 로고
    • Successful low toxicity hematopoietic stem cell transplantation for high-risk adult chronic granulomatous disease patients
    • Gungor T, Halter J, Klink A., et al Successful low toxicity hematopoietic stem cell transplantation for high-risk adult chronic granulomatous disease patients. Transplantation 2005; 79: 1596-606.
    • (2005) Transplantation , vol.79 , pp. 1596-1606
    • Gungor, T.1    Halter, J.2    Klink, A.3
  • 26
    • 11244284216 scopus 로고    scopus 로고
    • Improved survival after unrelated donor bone marrow transplantation in children with primary immunodeficiency using a reduced-intensity conditioning regimen
    • Rao K, Amrolia PJ, Jones A, et al Improved survival after unrelated donor bone marrow transplantation in children with primary immunodeficiency using a reduced-intensity conditioning regimen. Blood 2005; 105: 879-85.
    • (2005) Blood , vol.105 , pp. 879-885
    • Rao, K.1    Amrolia, P.J.2    Jones, A.3
  • 27
    • 0027934151 scopus 로고
    • Busulfan availability
    • Hassan M, Ljungman P, Bolme P., et al Busulfan availability. Blood 1994; 84: 2144-50.
    • (1994) Blood , vol.84 , pp. 2144-2150
    • Hassan, M.1    Ljungman, P.2    Bolme, P.3
  • 28
    • 0034882642 scopus 로고    scopus 로고
    • The pharmacodynamic effect of busulfan in the P39 myeloid cell line in vitro
    • Hassan Z, Hassan M, Hellstrom-Lindberg E. The pharmacodynamic effect of busulfan in the P39 myeloid cell line in vitro. Leukemia 2001; 15: 1240-47.
    • (2001) Leukemia , vol.15 , pp. 1240-1247
    • Hassan, Z.1    Hassan, M.2    Hellstrom-Lindberg, E.3
  • 29
    • 0036670854 scopus 로고    scopus 로고
    • The effect of modulation of glutathione cellular content on busulphan-induced cytotoxicity on hematopoietic cells in vitro and in vivo
    • Hassan Z, Hellstrom-Lindberg E, Alsadi S., Edgren M, Hagglund H, Hassan M. The effect of modulation of glutathione cellular content on busulphan-induced cytotoxicity on hematopoietic cells in vitro and in vivo. Bone Marrow Transplant 2002; 30: 141-47.
    • (2002) Bone Marrow Transplant , vol.30 , pp. 141-147
    • Hassan, Z.1    Hellstrom-Lindberg, E.2    Alsadi, S.3    Edgren, M.4    Hagglund, H.5    Hassan, M.6
  • 30
    • 77958193839 scopus 로고    scopus 로고
    • Impact of in vivo alemtuzumab dose before reduced intensity conditioning and HLA-identical sibling stem cell transplantation: Pharmacokinetics, GVHD, and immune reconstitution
    • Chakraverty R, Orti G, Roughton M., et al Impact of in vivo alemtuzumab dose before reduced intensity conditioning and HLA-identical sibling stem cell transplantation: pharmacokinetics, GVHD, and immune reconstitution. Blood 2010; 116: 3080-88.
    • (2010) Blood , vol.116 , pp. 3080-3088
    • Chakraverty, R.1    Orti, G.2    Roughton, M.3
  • 31
    • 75149125212 scopus 로고    scopus 로고
    • High burden of late effects after haematopoietic stem cell transplantation in childhood: A single-centre study
    • Bresters D, van Gils IC, Kollen WJ, et al High burden of late effects after haematopoietic stem cell transplantation in childhood: a single-centre study. Bone Marrow Transplant 2010; 45: 79-85.
    • (2010) Bone Marrow Transplant , vol.45 , pp. 79-85
    • Bresters, D.1    Van Gils, I.C.2    Kollen, W.J.3
  • 32
    • 84885405823 scopus 로고    scopus 로고
    • Favourable outcome after reduced-toxicity conditioning with high-dose fludarabine, serotherapy and low-dose/targeted busulfan in 74 children and adults with non-malignant diseases
    • Gungor T, Albert M, Slatter M., et al Favourable outcome after reduced-toxicity conditioning with high-dose fludarabine, serotherapy and low-dose/targeted busulfan in 74 children and adults with non-malignant diseases. Bone Marrow Transplant 2012; 47: S67-68.
    • (2012) Bone Marrow Transplant , vol.47
    • Gungor, T.1    Albert, M.2    Slatter, M.3


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