Gene and protein therapies utilizing VEGF for ALS

Pharmacology and Therapeutics

Volumn 141, Issue 3, 2014, Pages 261-271

  Keifer, Orion P ^a   O'Connor, Deirdre M ^a   Boulis, Nicholas M ^a  

^a EMORY UNIVERSITY SCHOOL OF MEDICINE   (United States)

Author keywords

ALS; Clinical trials; Gene therapy; Protein therapy; VEGF

Indexed keywords

PLACENTAL GROWTH FACTOR; VASCULOTROPIN A; VASCULOTROPIN B; VASCULOTROPIN C; VASCULOTROPIN D; VASCULOTROPIN RECEPTOR;

AMYOTROPHIC LATERAL SCLEROSIS; DRUG EFFECT; GENE DELIVERY SYSTEM; GENE THERAPY; HUMAN; NONHUMAN; OUTCOME ASSESSMENT; PRIORITY JOURNAL; REVIEW; STEM CELL;

AAV; ADENO-ASSOCIATED VIRUS; ALS; AMYOTROPHIC LATERAL SCLEROSIS; CENTRAL NERVOUS SYSTEM; CLINICAL TRIALS; CNS; FIG4; FRONTOTEMPORAL DEMENTIA; FTD; FUS; FUSED IN SARCOMA; GENE THERAPY; HRE; HYPOXIA RESPONSE ELEMENT; ICV; IGF-1; INSULIN-LIKE GROWTH FACTOR 1; INTRACEREBROVENTRICULAR; NEUROPILIN; NFΚB; NRP; NUCLEAR FACTOR KAPPA-LIGHT-CHAIN-ENHANCER OF ACTIVATED B CELLS; PLACENTAL GROWTH FACTOR; PLGF; POLYPHOSPHOINOSITIDE PHOSPHATASE; PROTEIN THERAPY; SENATAXIN; SETX; SOD1; SUPEROXIDE DISMUTASE 1; TAR DNA-BINDING DOMAIN PROTEIN; TDP43; UBIQUITIN-LIKE PROTEIN UBIQUILIN 2; UBQLN2; UNTRANSLATED REGION; UTR; VASCULAR ENDOTHELIA GROWTH FACTOR RECEPTOR; VASCULAR ENDOTHELIAL GROWTH FACTOR; VEGF; VEGFR;

AMYOTROPHIC LATERAL SCLEROSIS; ANIMALS; CLINICAL TRIALS AS TOPIC; DISEASE MODELS, ANIMAL; DRUG DESIGN; GENE EXPRESSION REGULATION; GENETIC THERAPY; HUMANS; MICE; PROTEINS; RECEPTORS, VASCULAR ENDOTHELIAL GROWTH FACTOR; VASCULAR ENDOTHELIAL GROWTH FACTOR A;

EID: 84892370972     PISSN: 01637258     EISSN: 1879016X     Source Type: Journal    
DOI: 10.1016/j.pharmthera.2013.10.009     Document Type: Review

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