The phenotype of dysferlin-deficient mice is not rescued by adeno-associated virus-mediated transfer of anoctamin 5.

Human gene therapy. Clinical development

Volumn 24, Issue 2, 2013, Pages 65-76

  Monjaret, François ^a   Suel Petat, Laurence ^b   Bourg Alibert, Nathalie ^b   Vihola, Anna ^b   Marchand, Sylvie ^b   Roudaut, Carinne ^b   Gicquel, Evelyne ^b   Udd, Bjarne ^b   Richard, Isabelle ^b   Charton, Karine ^b  

^a CNRS   (France)

^b NONE

Author keywords

[No Author keywords available]

Indexed keywords

ANO5 PROTEIN, HUMAN; CHLORIDE CHANNEL; DYSF PROTEIN, MOUSE; ISOPROTEIN; MEMBRANE PROTEIN;

ADENO ASSOCIATED VIRUS; ANIMAL; ARTICLE; C57BL MOUSE; CELL LINE; DOWN REGULATION; GENE TRANSFER; GENE VECTOR; GENETICS; HUMAN; KNOCKOUT MOUSE; LIMB GIRDLE MUSCULAR DYSTROPHY; METABOLISM; MOUSE; PATHOLOGY; PHENOTYPE; SKELETAL MUSCLE;

ANIMALS; CELL LINE; CHLORIDE CHANNELS; DEPENDOVIRUS; DOWN-REGULATION; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HUMANS; MEMBRANE PROTEINS; MICE; MICE, INBRED C57BL; MICE, KNOCKOUT; MUSCLE, SKELETAL; MUSCULAR DYSTROPHIES, LIMB-GIRDLE; PHENOTYPE; PROTEIN ISOFORMS;

EID: 84886682809     PISSN: None     EISSN: 23248645     Source Type: None    
DOI: 10.1089/humc.2012.217     Document Type: Article

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