Treatment of hip dysplasia in patients with mucopolysaccharidosis type i after hematopoietic stem cell transplantation: Results of an international consensus procedure

Orphanet Journal of Rare Diseases

Volumn 8, Issue 1, 2013, Pages

  Langereis, Eveline J ^a   Borgo, Andrea ^b   Crushell, Ellen ^c   Harmatz, Paul R ^d   Van Hasselt, Peter M ^e   Jones, Simon A ^f   Kelly, Paula M ^g   Lampe, Christina ^h   Van Der Lee, Johanna H ^a   Odent, Thierry ⁱ   Sakkers, Ralph ^e   Scarpa, Maurizio ^b   Schafroth, Matthias U ^a   Struijs, Peter A ^a   Valayannopoulos, Vassili ^j   White, Klane K ^k   Wijburg, Frits A ^a  

^a UNIVERSITY OF AMSTERDAM   (Netherlands)

^b UNIVERSITY OF PADOVA   (Italy)

^c CHILDREN S UNIVERSITY HOSPITAL   (Ireland)

^d CHILDREN S HOSPITAL OAKLAND   (United States)

^e UNIVERSITY MEDICAL CENTER UTRECHT   (Netherlands)

^f MANCHESTER UNIVERSITY NHS FOUNDATION TRUST   (United Kingdom)

^g OUR LADY S CHILDREN S HOSPITAL   (Ireland)

^h JOHANNES GUTENBERG UNIVERSITY   (Germany)

ⁱ HÔPITAL NECKER ENFANTS MALADES   (France)

^j UNIVERSITÉ PARIS DESCARTES   (France)

^k UNIVERSITY OF WASHINGTON   (United States)

more..

Author keywords

Consensus; Dysostosis multiplex; Hematopoietic stem cell transplantation; Hip dysplasia; Hurler syndrome; Mucopolysaccharidosis type I; Surgical treatment

Indexed keywords

LARONIDASE;

ACETABULAR OSTEOTOMY; ARTICLE; CHILD; CLINICAL DECISION MAKING; CONSENSUS; DELPHI STUDY; DISEASE COURSE; EARLY INTERVENTION; FEMALE; FEMUR OSTEOTOMY; FOLLOW UP; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HIP DYSPLASIA; HIP RADIOGRAPHY; HUMAN; HURLER SYNDROME; LIFE EXPECTANCY; MAJOR CLINICAL STUDY; MOTOR DYSFUNCTION; ORTHOPEDIC SURGEON; OSTEOTOMY; OUTCOME ASSESSMENT; PEDIATRICIAN; PELVIS OSTEOTOMY; PHENOTYPE; PLASTIC SURGERY; POSTOPERATIVE COMPLICATION; POSTOPERATIVE PAIN; PRACTICE GUIDELINE; PRESCHOOL CHILD; RANGE OF MOTION; RESPIRATORY TRACT INFECTION; SCHOOL CHILD; TOTAL HIP PROSTHESIS; TREATMENT DURATION;

HEMATOPOIETIC STEM CELL TRANSPLANTATION; HIP DISLOCATION; HUMANS; MUCOPOLYSACCHARIDOSIS I;

EID: 84884859064     PISSN: None     EISSN: 17501172     Source Type: Journal    
DOI: 10.1186/1750-1172-8-155     Document Type: Article

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