Strategies for more rapid translation of cellular therapies for children: A US perspective

Pediatrics

Volumn 132, Issue 2, 2013, Pages 351-358

  Sanchez, Rosa ^a,f   Silberstein, Leslie E ^b   Lindblad, Robert W ^c   Welniak, Lisbeth A ^d   Mondoro, Traci Heath ^d   Wagner, John E ^e  

^a BLOOD SYSTEMS RESEARCH INSTITUTE   (United States)

^b Center for Human Cell Therapy   (United States)

^c EMMES CORPORATION   (United States)

^d NATIONAL HEART LUNG AND BLOOD INSTITUTE   (United States)

^e UNIVERSITY OF MINNESOTA   (United States)

^f NONE   (United States)

Author keywords

Cell therapy; Pediatric clinical trials; Stem cell

Indexed keywords

ADRENOLEUKODYSTROPHY; ARTICLE; BETA THALASSEMIA; CELL THERAPY; CHILD; CHILDHOOD DISEASE; CHILDHOOD MORTALITY; CLINICAL TRIAL (TOPIC); FANCONI ANEMIA; FOLLOW UP; FOOD AND DRUG ADMINISTRATION; GENE THERAPY; HEALTH CARE COST; HEALTH CARE NEED; HEMATOLOGIC DISEASE; HUMAN; METHODOLOGY; MORBIDITY; PRIORITY JOURNAL; REGENERATIVE MEDICINE; SEVERE COMBINED IMMUNODEFICIENCY; SICKLE CELL ANEMIA; TRANSLATIONAL RESEARCH; UNITED STATES; WORKSHOP;

EID: 84882267516     PISSN: 00314005     EISSN: 10984275     Source Type: Journal    
DOI: 10.1542/peds.2012-3383     Document Type: Article

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