Transitioning outcome measures: Relationship between the CMTPedS and CMTNSv2 in children, adolescents, and young adults with Charcot-Marie-Tooth disease

Journal of the Peripheral Nervous System

Volumn 18, Issue 2, 2013, Pages 177-180

  Burns, Joshua ^a   Menezes, Manoj ^a   Finkel, Richard S ^b   Estilow, Tim ^c   Moroni, Isabella ^d   Pagliano, Emanuela ^d   Laurá, Matilde ^e,f   Muntoni, Francesco ^f   Herrmann, David N ^g   Eichinger, Kate ^g   Shy, Rosemary ^h,i   Pareyson, Davide ^d   Reilly, Mary M ^e   Shy, Michael E ^h,j  

^a UNIVERSITY OF SYDNEY   (Australia)

^b UNIVERSITY OF CENTRAL FLORIDA COLLEGE OF MEDICINE   (United States)

^c CHILDREN S HOSPITAL OF PHILADELPHIA   (United States)

^d DEPARTMENT OF NEUROSURGERY   (Italy)

^e UNIVERSITY COLLEGE LONDON   (United Kingdom)

^f GREAT ORMOND STREET HOSPITAL   (United Kingdom)

^g UNIVERSITY OF ROCHESTER MEDICAL CENTER   (United States)

^h UNIVERSITY OF IOWA   (United States)

ⁱ CHILDREN'S HOSPITAL OF MICHIGAN   (United States)

^j WAYNE STATE UNIVERSITY SCHOOL OF MEDICINE   (United States)

more..

Author keywords

clinical trial; inherited peripheral neuropathy; natural history; neuromuscular diseases; outcome assessment

Indexed keywords

ADOLESCENT; ADOLESCENT DISEASE; ADULT; ARTICLE; CHARCOT MARIE TOOTH NEUROPATHY SCORE; CHARCOT MARIE TOOTH PEDIATRIC SCALE; CHILD; CHILDHOOD DISEASE; DISABILITY; DISEASE SEVERITY; FEMALE; HEREDITARY MOTOR SENSORY NEUROPATHY; HUMAN; MAJOR CLINICAL STUDY; MALE; NAMED INVENTORIES, QUESTIONNAIRES AND RATING SCALES; OUTCOME ASSESSMENT; PHENOTYPE; PRESCHOOL CHILD; PRIORITY JOURNAL; SCHOOL CHILD;

ADOLESCENT; CHARCOT-MARIE-TOOTH DISEASE; CHILD; CHILD, PRESCHOOL; DISABILITY EVALUATION; FEMALE; HUMANS; MALE; PATIENT OUTCOME ASSESSMENT; SEVERITY OF ILLNESS INDEX; YOUNG ADULT;

EID: 84879398575     PISSN: 10859489     EISSN: 15298027     Source Type: Journal    
DOI: 10.1111/jns5.12024     Document Type: Article

References (10)

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